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In vivo lentiviral vector gene therapy to cure hereditary tyrosinemia type 1 and prevent development of precancerous and cancerous lesions.
Nicolas, Clara T; VanLith, Caitlin J; Hickey, Raymond D; Du, Zeji; Hillin, Lori G; Guthman, Rebekah M; Cao, William J; Haugo, Benjamin; Lillegard, Annika; Roy, Diya; Bhagwate, Aditya; O'Brien, Daniel; Kocher, Jean-Pierre; Kaiser, Robert A; Russell, Stephen J; Lillegard, Joseph B.
Afiliação
  • Nicolas CT; Department of Surgery, Mayo Clinic, Rochester, MN, USA.
  • VanLith CJ; Faculty of Medicine, University of Barcelona, Barcelona, Spain.
  • Hickey RD; Department of Surgery, University of Alabama Birmingham, Birmingham, AL, USA.
  • Du Z; Department of Surgery, Mayo Clinic, Rochester, MN, USA.
  • Hillin LG; Department of Surgery, Mayo Clinic, Rochester, MN, USA.
  • Guthman RM; Department of Molecular Medicine, Mayo Clinic, Rochester, MN, USA.
  • Cao WJ; Department of Surgery, Mayo Clinic, Rochester, MN, USA.
  • Haugo B; Department of Surgery, Mayo Clinic, Rochester, MN, USA.
  • Lillegard A; Department of Surgery, Mayo Clinic, Rochester, MN, USA.
  • Roy D; Medical College of Wisconsin, Wausau, WI, USA.
  • Bhagwate A; Department of Surgery, Mayo Clinic, Rochester, MN, USA.
  • O'Brien D; Department of Surgery, Mayo Clinic, Rochester, MN, USA.
  • Kocher JP; Department of Surgery, Mayo Clinic, Rochester, MN, USA.
  • Kaiser RA; Department of Surgery, Mayo Clinic, Rochester, MN, USA.
  • Russell SJ; Department of Biomedical Statistics and Informatics, Mayo Clinic, Rochester, MN, USA.
  • Lillegard JB; Department of Biomedical Statistics and Informatics, Mayo Clinic, Rochester, MN, USA.
Nat Commun ; 13(1): 5012, 2022 08 25.
Article em En | MEDLINE | ID: mdl-36008405

Texto completo: 1 Base de dados: MEDLINE Assunto principal: Lesões Pré-Cancerosas / Tirosinemias Idioma: En Ano de publicação: 2022 Tipo de documento: Article

Texto completo: 1 Base de dados: MEDLINE Assunto principal: Lesões Pré-Cancerosas / Tirosinemias Idioma: En Ano de publicação: 2022 Tipo de documento: Article