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Efficacy and safety clinical trial with efavirenz in patients diagnosed with adult Niemann-pick type C with cognitive impairment.
Gascón-Bayarri, Jordi; Simon, Petru Cristian; Llop, Roser; Carnaval, Thiago; Ledesma, María Dolores; Rico, Imma; Sánchez-Castañeda, Cristina; Campdelacreu-Fumadó, Jaume; Calvo-Malvar, Nahum; Cos, Mònica; de Lama, Eugenia; Cortés-Romera, Montserrat; Rodríguez-Bel, Laura; Pérez-Sousa, Celia; Cerdán Sánchez, María; Muelas, Nuria; Sevillano, María Dolores; Mir, Pablo; López de Munain, Adolfo; Ferrer, Anna; Videla, Sebastián.
Afiliação
  • Gascón-Bayarri J; Neurology Department, Bellvitge University Hospital, L'Hospitalet DE Llobregat, Barcelona, Spain.
  • Simon PC; Adult Lysosomal Diseases Clinical Expertise Unit, Bellvitge University Hospital, L'Hospitalet DE Llobregat, Barcelona, Spain.
  • Llop R; Bellvitge Biomedical Research Institute (IDIBELL), L'Hospitalet DE Llobregat, Barcelona, Spain.
  • Carnaval T; Department of Morphological Sciences, School of Medicine, Autonomous University of Barcelona, Bellaterra, Spain.
  • Ledesma MD; Clinical Pharmacology Department, Bellvitge University Hospital, L'Hospitalet de Llobregat, Barcelona, Spain.
  • Rico I; Clinical Pharmacology Department, Bellvitge University Hospital, L'Hospitalet de Llobregat, Barcelona, Spain.
  • Sánchez-Castañeda C; Pharmacology Unit, Department of Pathology and Experimental Therapeutics, School of Medicine and Health Sciences, IDIBELL, University of Barcelona, L'Hospitalet DE Llobregat, Barcelona, Spain.
  • Campdelacreu-Fumadó J; Severo Ochoa Molecular Biology Center (CSIC-UAM), Madrid, Spain.
  • Calvo-Malvar N; Neurology Department, Bellvitge University Hospital, L'Hospitalet DE Llobregat, Barcelona, Spain.
  • Cos M; Bellvitge Biomedical Research Institute (IDIBELL), L'Hospitalet DE Llobregat, Barcelona, Spain.
  • de Lama E; Neurology Department, Bellvitge University Hospital, L'Hospitalet DE Llobregat, Barcelona, Spain.
  • Cortés-Romera M; Bellvitge Biomedical Research Institute (IDIBELL), L'Hospitalet DE Llobregat, Barcelona, Spain.
  • Rodríguez-Bel L; Department of Clinical Psychology and Psychobiology, Neurosciences Institute, University of Barcelona, Barcelona, Spain.
  • Pérez-Sousa C; Neurology Department, Bellvitge University Hospital, L'Hospitalet DE Llobregat, Barcelona, Spain.
  • Cerdán Sánchez M; Bellvitge Biomedical Research Institute (IDIBELL), L'Hospitalet DE Llobregat, Barcelona, Spain.
  • Muelas N; Bellvitge Biomedical Research Institute (IDIBELL), L'Hospitalet DE Llobregat, Barcelona, Spain.
  • Sevillano MD; Neuroradiology Department, Bellvitge University Hospital, L'Hospitalet DE Llobregat, Spain.
  • Mir P; Bellvitge Biomedical Research Institute (IDIBELL), L'Hospitalet DE Llobregat, Barcelona, Spain.
  • López de Munain A; Neuroradiology Department, Bellvitge University Hospital, L'Hospitalet DE Llobregat, Spain.
  • Ferrer A; Bellvitge Biomedical Research Institute (IDIBELL), L'Hospitalet DE Llobregat, Barcelona, Spain.
  • Videla S; Neuroradiology Department, Bellvitge University Hospital, L'Hospitalet DE Llobregat, Spain.
Medicine (Baltimore) ; 101(48): e31471, 2022 Dec 02.
Article em En | MEDLINE | ID: mdl-36482560

Texto completo: 1 Base de dados: MEDLINE Assunto principal: Doença de Niemann-Pick Tipo C / Disfunção Cognitiva Idioma: En Ano de publicação: 2022 Tipo de documento: Article

Texto completo: 1 Base de dados: MEDLINE Assunto principal: Doença de Niemann-Pick Tipo C / Disfunção Cognitiva Idioma: En Ano de publicação: 2022 Tipo de documento: Article