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AAV2-Mediated Gene Therapy for Choroideremia: 5-Year Results and Alternate Anti-sense Oligonucleotide Therapy.
Zhai, Yi; Xu, Manlong; Radziwon, Alina; Dimopoulos, Ioannis S; Crichton, Paul; Mah, Rachel; MacLaren, Robert E; Somani, Rizwan; Tennant, Matthew T; MacDonald, Ian M.
Afiliação
  • Zhai Y; From the Department of Ophthalmology and Visual Sciences (Y.Z., M.X., A.R., R.S., M.T.T., I.M.M.), University of Alberta, Edmonton, Alberta, Canada.
  • Xu M; From the Department of Ophthalmology and Visual Sciences (Y.Z., M.X., A.R., R.S., M.T.T., I.M.M.), University of Alberta, Edmonton, Alberta, Canada.
  • Radziwon A; From the Department of Ophthalmology and Visual Sciences (Y.Z., M.X., A.R., R.S., M.T.T., I.M.M.), University of Alberta, Edmonton, Alberta, Canada; Department of Medical Genetics (A.R., I.M.M.), University of Alberta, Edmonton, Alberta, Canada.
  • Dimopoulos IS; Department of Ophthalmology (I.S.D., P.C., R.M.), University of Ottawa, Ottawa, Ontario, Canada.
  • Crichton P; Department of Ophthalmology (I.S.D., P.C., R.M.), University of Ottawa, Ottawa, Ontario, Canada.
  • Mah R; Department of Ophthalmology (I.S.D., P.C., R.M.), University of Ottawa, Ottawa, Ontario, Canada.
  • MacLaren RE; Nuffield Laboratory of Ophthalmology (R.E.M.), Department of Clinical Neurosciences, University of Oxford and NIHR Oxford Biomedical Research Centre, Oxfordshire, UK.
  • Somani R; From the Department of Ophthalmology and Visual Sciences (Y.Z., M.X., A.R., R.S., M.T.T., I.M.M.), University of Alberta, Edmonton, Alberta, Canada.
  • Tennant MT; From the Department of Ophthalmology and Visual Sciences (Y.Z., M.X., A.R., R.S., M.T.T., I.M.M.), University of Alberta, Edmonton, Alberta, Canada.
  • MacDonald IM; From the Department of Ophthalmology and Visual Sciences (Y.Z., M.X., A.R., R.S., M.T.T., I.M.M.), University of Alberta, Edmonton, Alberta, Canada; Department of Medical Genetics (A.R., I.M.M.), University of Alberta, Edmonton, Alberta, Canada. Electronic address: macdonal@ualberta.ca.
Am J Ophthalmol ; 248: 145-156, 2023 04.
Article em En | MEDLINE | ID: mdl-36581191

Texto completo: 1 Base de dados: MEDLINE Assunto principal: Coroideremia Idioma: En Ano de publicação: 2023 Tipo de documento: Article

Texto completo: 1 Base de dados: MEDLINE Assunto principal: Coroideremia Idioma: En Ano de publicação: 2023 Tipo de documento: Article