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N-Substituted l-Iminosugars for the Treatment of Sanfilippo Type B Syndrome.
De Pasquale, Valeria; Esposito, Anna; Scerra, Gianluca; Scarcella, Melania; Ciampa, Mariangela; Luongo, Antonietta; D'Alonzo, Daniele; Guaragna, Annalisa; D'Agostino, Massimo; Pavone, Luigi Michele.
Afiliação
  • De Pasquale V; Department of Veterinary Medicine and Animal Productions, University of Naples Federico II, Via F. Delpino 1, 80137 Naples, Italy.
  • Esposito A; Department of Chemical, Materials and Production Engineering, University of Naples Federico II, Piazzale V. Tecchio 80, 80125 Naples, Italy.
  • Scerra G; Department of Molecular Medicine and Medical Biotechnology, University of Naples Federico II, Via S. Pansini 5, 80131 Naples, Italy.
  • Scarcella M; Department of Molecular Medicine and Medical Biotechnology, University of Naples Federico II, Via S. Pansini 5, 80131 Naples, Italy.
  • Ciampa M; Department of Molecular Medicine and Medical Biotechnology, University of Naples Federico II, Via S. Pansini 5, 80131 Naples, Italy.
  • Luongo A; AORN Sant'Anna e San Sebastiano, Via F. Palasciano, 81100 Caserta, Italy.
  • D'Alonzo D; Department of Chemical Sciences, University of Naples Federico II, Via Cintia, 80126 Napoli, Italy.
  • Guaragna A; Department of Chemical, Materials and Production Engineering, University of Naples Federico II, Piazzale V. Tecchio 80, 80125 Naples, Italy.
  • D'Agostino M; Department of Molecular Medicine and Medical Biotechnology, University of Naples Federico II, Via S. Pansini 5, 80131 Naples, Italy.
  • Pavone LM; Department of Molecular Medicine and Medical Biotechnology, University of Naples Federico II, Via S. Pansini 5, 80131 Naples, Italy.
J Med Chem ; 66(3): 1790-1808, 2023 02 09.
Article em En | MEDLINE | ID: mdl-36696678

Texto completo: 1 Base de dados: MEDLINE Assunto principal: Mucopolissacaridose III Idioma: En Ano de publicação: 2023 Tipo de documento: Article

Texto completo: 1 Base de dados: MEDLINE Assunto principal: Mucopolissacaridose III Idioma: En Ano de publicação: 2023 Tipo de documento: Article