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Trials for Slowly Progressive Neurogenetic Diseases Need Surrogate Endpoints.
Reilly, Mary M; Herrmann, David N; Pareyson, Davide; Scherer, Steven S; Finkel, Richard S; Züchner, Stephan; Burns, Joshua; Shy, Michael E.
Afiliação
  • Reilly MM; Department of Neuromuscular Diseases, UCL Queen Square Institute of Neurology, London, UK.
  • Herrmann DN; Department of Neurology, University of Rochester, Rochester, NY.
  • Pareyson D; Unit of Rare Neurodegenerative and Neurometabolic Diseases, Department of Clinical Neurosciences, Fondazione IRRCCS Istituto Neurologico Carlo Besta, Milan, Italy.
  • Scherer SS; Department of Neurology, The Perelman School of Medicine at the University of Pennsylvania, Philadelphia, PA.
  • Finkel RS; Center for Experimental Neurotherapeutics, St. Jude Children's Research Hospital, Memphis, TN.
  • Züchner S; Dr. John T. Macdonald Foundation Department of Human Genetics and John P. Hussman Institute for Human Genomics, University of Miami Miller School of Medicine, Miami, FL.
  • Burns J; Sydney School of Health Sciences, University of Sydney, Sydney, Australia.
  • Shy ME; Department of Neurology, Carver College of Medicine, University of Iowa, Iowa, IA.
Ann Neurol ; 93(5): 906-910, 2023 05.
Article em En | MEDLINE | ID: mdl-36891823

Texto completo: 1 Base de dados: MEDLINE Assunto principal: Doenças do Sistema Nervoso Periférico / Doenças do Sistema Nervoso Idioma: En Ano de publicação: 2023 Tipo de documento: Article

Texto completo: 1 Base de dados: MEDLINE Assunto principal: Doenças do Sistema Nervoso Periférico / Doenças do Sistema Nervoso Idioma: En Ano de publicação: 2023 Tipo de documento: Article