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Development of a Biosimilar of Agalsidase Beta for the Treatment of Fabry Disease: Preclinical Evaluation.
van Kuilenburg, André B P; Hollak, Carla E M; Travella, Ana; Jacobs, Melisa; Gentilini, Lucas D; Leen, René; der Vlugt, Karen M M Ghauharali-van; Stet, Femke S Beers; Goorden, Susan M I; van der Veen, Sanne; Criscuolo, Marcelo; Papouchado, Mariana.
Afiliação
  • van Kuilenburg ABP; Amsterdam UMC location University of Amsterdam, Laboratory Genetic Metabolic Diseases F0-220, Meibergdreef 9, 1105 AZ, Amsterdam, The Netherlands. a.b.vankuilenburg@amsterdamumc.nl.
  • Hollak CEM; Amsterdam Gastroenterology Endocrinology Metabolism, Amsterdam, The Netherlands. a.b.vankuilenburg@amsterdamumc.nl.
  • Travella A; Amsterdam Gastroenterology Endocrinology Metabolism, Amsterdam, The Netherlands.
  • Jacobs M; Amsterdam UMC location University of Amsterdam, Endocrinology and Metabolism, Meibergdreef 9, Amsterdam, The Netherlands.
  • Gentilini LD; Medicine for Society, Platform at Amsterdam, UMC-University of Amsterdam, Amsterdam, The Netherlands.
  • Leen R; Biosidus S.A., Buenos Aires, Argentina.
  • der Vlugt KMMG; Biosidus S.A., Buenos Aires, Argentina.
  • Stet FSB; Biosidus S.A., Buenos Aires, Argentina.
  • Goorden SMI; Amsterdam UMC location University of Amsterdam, Laboratory Genetic Metabolic Diseases F0-220, Meibergdreef 9, 1105 AZ, Amsterdam, The Netherlands.
  • van der Veen S; Amsterdam Gastroenterology Endocrinology Metabolism, Amsterdam, The Netherlands.
  • Criscuolo M; Amsterdam UMC location University of Amsterdam, Laboratory Genetic Metabolic Diseases F0-220, Meibergdreef 9, 1105 AZ, Amsterdam, The Netherlands.
  • Papouchado M; Amsterdam Gastroenterology Endocrinology Metabolism, Amsterdam, The Netherlands.
Drugs R D ; 23(2): 141-153, 2023 Jun.
Article em En | MEDLINE | ID: mdl-37083901

Texto completo: 1 Base de dados: MEDLINE Assunto principal: Doença de Fabry / Medicamentos Biossimilares Idioma: En Ano de publicação: 2023 Tipo de documento: Article

Texto completo: 1 Base de dados: MEDLINE Assunto principal: Doença de Fabry / Medicamentos Biossimilares Idioma: En Ano de publicação: 2023 Tipo de documento: Article