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Rapid home therapy infusion of velaglucerase alfa in naïve patients with Gaucher disease.
Becker-Cohen, Michal; Revel-Vilk, Shoshana; Frydman, Dafna; Dinur, Tama; Tiomkin, Maayan; Istaiti, Majdolen; Arbel, Naama; Bauer, Peter; Cozma, Claudia; Rolfs, Arndt; Szer, Jeff; Zimran, Ari.
Afiliação
  • Becker-Cohen M; Gaucher Unit, Shaare Zedek Medical Centre, Jerusalem, Israel.
  • Revel-Vilk S; Gaucher Unit, Shaare Zedek Medical Centre, Jerusalem, Israel.
  • Frydman D; Faculty of Medicine, Hebrew University of Jerusalem, Jerusalem, Israel.
  • Dinur T; Gaucher Unit, Shaare Zedek Medical Centre, Jerusalem, Israel.
  • Tiomkin M; Gaucher Unit, Shaare Zedek Medical Centre, Jerusalem, Israel.
  • Istaiti M; Gaucher Unit, Shaare Zedek Medical Centre, Jerusalem, Israel.
  • Arbel N; Gaucher Unit, Shaare Zedek Medical Centre, Jerusalem, Israel.
  • Bauer P; Medison Pharma, Petah Tikva, Israel.
  • Cozma C; Centogene AG, Rostock, Germany.
  • Rolfs A; Centogene AG, Rostock, Germany.
  • Szer J; Department of Neurology and Psychiatry, Medical Faculty, University of Rostock, Rostock, Germany.
  • Zimran A; Arcensus GmbH, Rostock, Germany.
Intern Med J ; 54(3): 398-403, 2024 Mar.
Article em En | MEDLINE | ID: mdl-37493453

Texto completo: 1 Base de dados: MEDLINE Assunto principal: Doença de Gaucher Idioma: En Ano de publicação: 2024 Tipo de documento: Article

Texto completo: 1 Base de dados: MEDLINE Assunto principal: Doença de Gaucher Idioma: En Ano de publicação: 2024 Tipo de documento: Article