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Long-term treatment with ganaxolone for seizures associated with cyclin-dependent kinase-like 5 deficiency disorder: Two-year open-label extension follow-up.
Olson, Heather E; Amin, Sam; Bahi-Buisson, Nadia; Devinsky, Orrin; Marsh, Eric D; Pestana-Knight, Elia; Rajaraman, Rajsekar R; Aimetti, Alex A; Rybak, Eva; Kong, Fanhui; Miller, Ian; Hulihan, Joseph; Demarest, Scott.
Afiliação
  • Olson HE; Department of Neurology, Division of Epilepsy and Clinical Neurophysiology, Boston Children's Hospital and Harvard Medical School, Boston, Massachusetts, USA.
  • Amin S; University Hospitals Bristol and Weston, Bristol, UK.
  • Bahi-Buisson N; Pediatric Neurology, Necker Enfants Malades University Hospital, Paris, France.
  • Devinsky O; New York University Langone Comprehensive Epilepsy Center, New York, New York, USA.
  • Marsh ED; Departments of Neurology and Pediatrics, University of Pennsylvania Perelman School of Medicine and Division of Neurology, Children's Hospital of Philadelphia, Philadelphia, Pennsylvania, USA.
  • Pestana-Knight E; Epilepsy Center, Cleveland Clinic, Cleveland, Ohio, USA.
  • Rajaraman RR; UCLA Mattel Children's Hospital, Los Angeles, California, USA.
  • Aimetti AA; Marinus Pharmaceuticals, Inc., Radnor, Pennsylvania, USA.
  • Rybak E; Marinus Pharmaceuticals, Inc., Radnor, Pennsylvania, USA.
  • Kong F; Marinus Pharmaceuticals, Inc., Radnor, Pennsylvania, USA.
  • Miller I; Marinus Pharmaceuticals, Inc., Radnor, Pennsylvania, USA.
  • Hulihan J; Marinus Pharmaceuticals, Inc., Radnor, Pennsylvania, USA.
  • Demarest S; Department of Pediatrics and Neurology, University of Colorado School of Medicine, Precision Medicine Institute, Children's Hospital Colorado, Aurora, Colorado, USA.
Epilepsia ; 65(1): 37-45, 2024 Jan.
Article em En | MEDLINE | ID: mdl-37950390

Texto completo: 1 Base de dados: MEDLINE Assunto principal: Pregnanolona / Espasmos Infantis / Epilepsia Tônico-Clônica / Síndromes Epilépticas / Anticonvulsivantes Idioma: En Ano de publicação: 2024 Tipo de documento: Article

Texto completo: 1 Base de dados: MEDLINE Assunto principal: Pregnanolona / Espasmos Infantis / Epilepsia Tônico-Clônica / Síndromes Epilépticas / Anticonvulsivantes Idioma: En Ano de publicação: 2024 Tipo de documento: Article