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Safety, pharmacokinetics and efficacy of selumetinib in Chinese adult and paediatric patients with neurofibromatosis type 1 and inoperable plexiform neurofibromas: The primary analysis of a phase 1 open-label study.
Wang, Zhichao; Zhang, Xin; Li, Chunyan; Liu, Yangbo; Ge, Xiaoyun; Zhao, Jiajia; Yuan, Xiaojun; Li, Qingfeng.
Afiliação
  • Wang Z; Shanghai Ninth People's Hospital Affiliated to Shanghai JiaoTong University School of Medicine, Shanghai, China.
  • Zhang X; Xinhua Hospital Affiliated to Shanghai JiaoTong University School of Medicine, Shanghai, China.
  • Li C; AstraZeneca Global R&D (China) Co. Ltd., Shanghai, China.
  • Liu Y; AstraZeneca Global R&D (China) Co. Ltd., Shanghai, China.
  • Ge X; AstraZeneca Global R&D (China) Co. Ltd., Shanghai, China.
  • Zhao J; AstraZeneca Global R&D (China) Co. Ltd., Shanghai, China.
  • Yuan X; Xinhua Hospital Affiliated to Shanghai JiaoTong University School of Medicine, Shanghai, China.
  • Li Q; Shanghai Ninth People's Hospital Affiliated to Shanghai JiaoTong University School of Medicine, Shanghai, China.
Clin Transl Med ; 14(3): e1589, 2024 03.
Article em En | MEDLINE | ID: mdl-38456222

Texto completo: 1 Base de dados: MEDLINE Assunto principal: Neurofibromatose 1 / Neurofibroma Plexiforme Idioma: En Ano de publicação: 2024 Tipo de documento: Article

Texto completo: 1 Base de dados: MEDLINE Assunto principal: Neurofibromatose 1 / Neurofibroma Plexiforme Idioma: En Ano de publicação: 2024 Tipo de documento: Article