Hemophilia Gene Therapy: Another Blessing or Another Curse?
Mo Med
; 121(3): 231-234, 2024.
Article
em En
| MEDLINE
| ID: mdl-38854602
ABSTRACT
Medical therapies for hemophilia patients over the past 60 years have included several blessings and a curse. The long-sought cure with gene therapy may have finally arrived. Unfortunately, preclinical animal models are now raising concerns for genotoxicity with gene therapy. Although no cancers have been detected in humans, it may be a few decades before we know if gene therapy for hemophilia is another blessing, or another curse.
Texto completo:
1
Base de dados:
MEDLINE
Assunto principal:
Terapia Genética
/
Hemofilia A
Idioma:
En
Ano de publicação:
2024
Tipo de documento:
Article