Detalhe da pesquisa
1.
Current avenues of gene therapy in Pompe disease.
Curr Opin Neurol
; 36(5): 464-473, 2023 10 01.
Artigo
em Inglês
| MEDLINE | ID: mdl-37639402
2.
Sensitivity of Pharmacokinetics to Differences in the Particle Size Distribution for Formulations of Locally Acting Mometasone Furoate Suspension-Based Nasal Sprays.
Mol Pharm
; 20(11): 5690-5700, 2023 11 06.
Artigo
em Inglês
| MEDLINE | ID: mdl-37773975
3.
Secondary hemophagocytic lymphohistiocytosis following Zolgensma therapy: An evolving story on the innate response to systemic gene therapy.
Mol Ther
; 30(12): 3503-3504, 2022 12 07.
Artigo
em Inglês
| MEDLINE | ID: mdl-36436512
4.
Twelve Tips to Succeed as Health Profession Clinical Educator in Resource-Limited Settings.
Adv Med Educ Pract
; 15: 201-206, 2024.
Artigo
em Inglês
| MEDLINE | ID: mdl-38505497
5.
Longitudinal changes of swallowing safety and efficiency in infants with spinal muscular atrophy who received disease modifying therapies.
Pediatr Pulmonol
; 59(5): 1364-1371, 2024 May.
Artigo
em Inglês
| MEDLINE | ID: mdl-38358081
6.
ATS core curriculum 2023. Pediatric pulmonary medicine: Respiratory disorders in infants.
Pediatr Pulmonol
; 59(6): 1552-1568, 2024 Jun.
Artigo
em Inglês
| MEDLINE | ID: mdl-38545994
7.
Thrombotic microangiopathy following systemic AAV administration is dependent on anti-capsid antibodies.
J Clin Invest
; 134(1)2024 Jan 02.
Artigo
em Inglês
| MEDLINE | ID: mdl-37988172
8.
Diaphragm pacing and independent breathing in individuals with severe Pompe disease.
Front Rehabil Sci
; 4: 1184031, 2023.
Artigo
em Inglês
| MEDLINE | ID: mdl-37583873
9.
Polysomnography findings in children with spinal muscular atrophy after onasemnogene-abeparvovec.
Sleep Med
; 101: 234-237, 2023 01.
Artigo
em Inglês
| MEDLINE | ID: mdl-36442421
10.
ATS Core Curriculum 2022. Pediatric Pulmonary Medicine: Updates in pediatric neuromuscular disease.
Pediatr Pulmonol
; 58(7): 1866-1874, 2023 Jul.
Artigo
em Inglês
| MEDLINE | ID: mdl-37144867
11.
Addressing the implementation gap in advanced therapeutics for spinal muscular atrophy in the era of newborn screening programs.
Front Neurol
; 13: 1064194, 2022.
Artigo
em Inglês
| MEDLINE | ID: mdl-36578307
12.
An Unusual Case of Noisy Breathing in an Infant.
J Clin Sleep Med
; 15(1): 149-152, 2019 01 15.
Artigo
em Inglês
| MEDLINE | ID: mdl-30621832
13.
Performance of International Medical Graduates in Pediatric Residency: A Study of Peer and Faculty Perceptions.
Acad Pediatr
; 18(7): 728-732, 2018.
Artigo
em Inglês
| MEDLINE | ID: mdl-30056222
14.
International Medical Graduates in Pediatrics: Should I Stay or Should I Go?
JAMA Pediatr
; 173(3): 217-218, 2019 Mar 01.
Artigo
em Inglês
| MEDLINE | ID: mdl-30667478
15.
Treatment of severe persistent asthma with IL-6 receptor blockade.
J Allergy Clin Immunol Pract
; 7(5): 1639-1642.e4, 2019.
Artigo
em Inglês
| MEDLINE | ID: mdl-30885880