Haematopoietic cell transplantation (HCT) in combination with enzyme replacement therapy (ERT) in patients with Hurler syndrome.

Cox-Brinkman, J; Boelens, J-J; Wraith, J E; O'meara, A; Veys, P; Wijburg, F A; Wulffraat, N; Wynn, R F

Cox-Brinkman, J; Boelens, J-J; Wraith, J E; O'meara, A; Veys, P; Wijburg, F A; Wulffraat, N; Wynn, R F.

Affiliation

Cox-Brinkman J; Department of Paediatrics, Emma Children's Hospital, Academic Medical Center, Amsterdam, The Netherlands.

Bone Marrow Transplant ; 38(1): 17-21, 2006 Jul.

Article in En | MEDLINE | ID: mdl-16715104

Subject(s)

Hematopoietic Stem Cell Transplantation; Iduronidase/therapeutic use; Mucopolysaccharidosis I/therapy; Child, Preschool; Combined Modality Therapy/methods; Follow-Up Studies; Graft vs Host Disease/diagnosis; Graft vs Host Disease/therapy; Humans; Iduronidase/administration & dosage; Infant; Mucopolysaccharidosis I/diagnosis; Recombinant Proteins/administration & dosage; Recombinant Proteins/therapeutic use; Treatment Outcome

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Collection: 01-internacional Database: MEDLINE Main subject: Mucopolysaccharidosis I / Hematopoietic Stem Cell Transplantation / Iduronidase Type of study: Clinical_trials / Diagnostic_studies / Observational_studies / Prognostic_studies / Risk_factors_studies Limits: Child, preschool / Humans / Infant Language: En Journal: Bone Marrow Transplant Journal subject: TRANSPLANTE Year: 2006 Type: Article Affiliation country: Netherlands

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