Emotional impact of genetic trials in progressive paediatric disorders: a dose-ranging exon-skipping trial in Duchenne muscular dystrophy.

Garralda, M E; McConachie, H; Le Couteur, A; Sriranjan, S; Chakrabarti, I; Cirak, S; Guglieri, M; Bushby, K; Muntoni, F

Garralda, M E; McConachie, H; Le Couteur, A; Sriranjan, S; Chakrabarti, I; Cirak, S; Guglieri, M; Bushby, K; Muntoni, F.

Affiliation

Garralda ME; Academic Unit of Child and Adolescent Psychiatry, Imperial College London, London, UK. e.garralda@imperial.ac.uk

Child Care Health Dev ; 39(3): 449-55, 2013 May.

Article in En | MEDLINE | ID: mdl-22676208

Subject(s)

Affective Symptoms/etiology; Genetic Therapy/psychology; Muscular Dystrophy, Duchenne/therapy; Child; Dose-Response Relationship, Drug; Family Health; Genetic Therapy/methods; Humans; Male; Morpholinos/genetics; Muscular Dystrophy, Duchenne/genetics; Muscular Dystrophy, Duchenne/psychology; Oligonucleotides/administration & dosage; Oligonucleotides/therapeutic use; Parents/psychology; Psychiatric Status Rating Scales; Psychometrics; Stress, Psychological/etiology

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Full text: 1 Collection: 01-internacional Database: MEDLINE Main subject: Genetic Therapy / Muscular Dystrophy, Duchenne / Affective Symptoms Type of study: Clinical_trials / Etiology_studies / Prognostic_studies / Qualitative_research Limits: Child / Humans / Male Language: En Journal: Child Care Health Dev Year: 2013 Type: Article Affiliation country: United kingdom

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