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Comparison of outcomes of hematopoietic stem cell transplantation without chemotherapy conditioning by using matched sibling and unrelated donors for treatment of severe combined immunodeficiency.
Dvorak, Christopher C; Hassan, Amel; Slatter, Mary A; Hönig, Manfred; Lankester, Arjan C; Buckley, Rebecca H; Pulsipher, Michael A; Davis, Jeffrey H; Güngör, Tayfun; Gabriel, Melissa; Bleesing, Jacob H; Bunin, Nancy; Sedlacek, Petr; Connelly, James A; Crawford, David F; Notarangelo, Luigi D; Pai, Sung-Yun; Hassid, Jake; Veys, Paul; Gennery, Andrew R; Cowan, Morton J.
Affiliation
  • Dvorak CC; Division of Pediatric Allergy, Immunology, and Blood and Marrow Transplant, Benioff Children's Hospital, University of California San Francisco, San Francisco, Calif. Electronic address: dvorakc@peds.ucsf.edu.
  • Hassan A; Centre for Immunodeficiency, Molecular Immunology Unit, UCL Institute of Child Health, London, United Kingdom.
  • Slatter MA; Institute of Cellular Medicine, Newcastle University, Newcastle upon Tyne, United Kingdom.
  • Hönig M; Department of Pediatrics, University Medical Center, Ulm, Germany.
  • Lankester AC; Department of Pediatrics, Leiden University Medical Center, Leiden, The Netherlands.
  • Buckley RH; Departments of Pediatrics and Immunology, Duke University Medical Center, Durham, NC.
  • Pulsipher MA; Division of Hematology and Hematologic Malignancies, Primary Children's Hospital, University of Utah School of Medicine/Huntsman Cancer Institute, Salt Lake City, Utah.
  • Davis JH; Hematology/Oncology/BMT Program, British Columbia Children's Hospital, Vancouver, British Columbia, Canada.
  • Güngör T; University Children's Hospital, Stem Cell Transplantation Department, Zurich, Switzerland.
  • Gabriel M; Oncology Department, The Children's Hospital at Westmead, Westmead, Australia.
  • Bleesing JH; Department of Pediatrics, Cincinnati Children's Hospital Medical Center, Cincinnati, Ohio.
  • Bunin N; Division of Oncology, Department of Pediatrics, Children's Hospital of Philadelphia, Philadelphia, Pa.
  • Sedlacek P; Department of Pediatric Hematology and Oncology, Teaching Hospital Motol, Prague, Czech Republic.
  • Connelly JA; Division of Pediatric Hematology-Oncology, University of Michigan, Ann Arbor, Mich.
  • Crawford DF; Department of Pediatrics, University of Oklahoma, Oklahoma City, Okla.
  • Notarangelo LD; Division of Immunology and The Manton Center for Orphan Disease Research, Children's Hospital Boston, Harvard Medical School, Boston, Mass.
  • Pai SY; Division of Hematology and Oncology, Boston Children's Hospital, and the Department of Pediatric Oncology, Dana-Farber Cancer Institute, Boston, Mass.
  • Hassid J; Division of Pediatric Allergy, Immunology, and Blood and Marrow Transplant, Benioff Children's Hospital, University of California San Francisco, San Francisco, Calif.
  • Veys P; Centre for Immunodeficiency, Molecular Immunology Unit, UCL Institute of Child Health, London, United Kingdom.
  • Gennery AR; Institute of Cellular Medicine, Newcastle University, Newcastle upon Tyne, United Kingdom.
  • Cowan MJ; Division of Pediatric Allergy, Immunology, and Blood and Marrow Transplant, Benioff Children's Hospital, University of California San Francisco, San Francisco, Calif.
J Allergy Clin Immunol ; 134(4): 935-943.e15, 2014 Oct.
Article in En | MEDLINE | ID: mdl-25109802

Full text: 1 Collection: 01-internacional Database: MEDLINE Main subject: B-Lymphocytes / T-Lymphocytes / Severe Combined Immunodeficiency / Hematopoietic Stem Cell Transplantation / Siblings / Unrelated Donors Type of study: Diagnostic_studies / Etiology_studies / Observational_studies / Risk_factors_studies Limits: Adult / Child / Female / Humans / Infant / Male / Newborn Country/Region as subject: America do norte / Europa / Oceania Language: En Journal: J Allergy Clin Immunol Year: 2014 Type: Article

Full text: 1 Collection: 01-internacional Database: MEDLINE Main subject: B-Lymphocytes / T-Lymphocytes / Severe Combined Immunodeficiency / Hematopoietic Stem Cell Transplantation / Siblings / Unrelated Donors Type of study: Diagnostic_studies / Etiology_studies / Observational_studies / Risk_factors_studies Limits: Adult / Child / Female / Humans / Infant / Male / Newborn Country/Region as subject: America do norte / Europa / Oceania Language: En Journal: J Allergy Clin Immunol Year: 2014 Type: Article