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Preclinical evaluation of RNAi as a treatment for transthyretin-mediated amyloidosis.
Butler, James S; Chan, Amy; Costelha, Susete; Fishman, Shannon; Willoughby, Jennifer L S; Borland, Todd D; Milstein, Stuart; Foster, Donald J; Gonçalves, Paula; Chen, Qingmin; Qin, June; Bettencourt, Brian R; Sah, Dinah W; Alvarez, Rene; Rajeev, Kallanthottathil G; Manoharan, Muthiah; Fitzgerald, Kevin; Meyers, Rachel E; Nochur, Saraswathy V; Saraiva, Maria J; Zimmermann, Tracy S.
Affiliation
  • Butler JS; a Alnylam Pharmaceuticals , Cambridge , MA , USA .
  • Chan A; a Alnylam Pharmaceuticals , Cambridge , MA , USA .
  • Costelha S; b Instituto de Investigação e Inovação em Saúde, Universidade do Porto , Porto , Portugal .
  • Fishman S; c Molecular Neurobiology, IBMC - Institute for Molecular and Cell Biology Porto , Porto , Portugal.
  • Willoughby JL; a Alnylam Pharmaceuticals , Cambridge , MA , USA .
  • Borland TD; a Alnylam Pharmaceuticals , Cambridge , MA , USA .
  • Milstein S; a Alnylam Pharmaceuticals , Cambridge , MA , USA .
  • Foster DJ; a Alnylam Pharmaceuticals , Cambridge , MA , USA .
  • Gonçalves P; a Alnylam Pharmaceuticals , Cambridge , MA , USA .
  • Chen Q; b Instituto de Investigação e Inovação em Saúde, Universidade do Porto , Porto , Portugal .
  • Qin J; c Molecular Neurobiology, IBMC - Institute for Molecular and Cell Biology Porto , Porto , Portugal.
  • Bettencourt BR; a Alnylam Pharmaceuticals , Cambridge , MA , USA .
  • Sah DW; a Alnylam Pharmaceuticals , Cambridge , MA , USA .
  • Alvarez R; a Alnylam Pharmaceuticals , Cambridge , MA , USA .
  • Rajeev KG; a Alnylam Pharmaceuticals , Cambridge , MA , USA .
  • Manoharan M; a Alnylam Pharmaceuticals , Cambridge , MA , USA .
  • Fitzgerald K; a Alnylam Pharmaceuticals , Cambridge , MA , USA .
  • Meyers RE; a Alnylam Pharmaceuticals , Cambridge , MA , USA .
  • Nochur SV; a Alnylam Pharmaceuticals , Cambridge , MA , USA .
  • Saraiva MJ; a Alnylam Pharmaceuticals , Cambridge , MA , USA .
  • Zimmermann TS; a Alnylam Pharmaceuticals , Cambridge , MA , USA .
Amyloid ; 23(2): 109-18, 2016 Jun.
Article in En | MEDLINE | ID: mdl-27033334

Full text: 1 Collection: 01-internacional Database: MEDLINE Main subject: Prealbumin / RNA, Messenger / Amyloid Neuropathies, Familial / RNA, Small Interfering / Liver Limits: Animals / Female / Humans / Male Language: En Journal: Amyloid Journal subject: BIOQUIMICA Year: 2016 Type: Article Affiliation country: United States

Full text: 1 Collection: 01-internacional Database: MEDLINE Main subject: Prealbumin / RNA, Messenger / Amyloid Neuropathies, Familial / RNA, Small Interfering / Liver Limits: Animals / Female / Humans / Male Language: En Journal: Amyloid Journal subject: BIOQUIMICA Year: 2016 Type: Article Affiliation country: United States