AAV-mediated gene therapy in Dystrophin-Dp71 deficient mouse leads to blood-retinal barrier restoration and oedema reabsorption.
Hum Mol Genet
; 25(14): 3070-3079, 2016 07 15.
Article
in En
| MEDLINE
| ID: mdl-27288449
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Collection:
01-internacional
Database:
MEDLINE
Main subject:
Blood-Retinal Barrier
/
Genetic Therapy
/
Dystrophin
/
Edema
Limits:
Animals
/
Humans
Language:
En
Journal:
Hum Mol Genet
Journal subject:
BIOLOGIA MOLECULAR
/
GENETICA MEDICA
Year:
2016
Type:
Article
Affiliation country:
France