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Assessing mNIS+7Ionis and international neurologists' proficiency in a familial amyloidotic polyneuropathy trial.
Dyck, Peter J; Kincaid, John C; Dyck, P James B; Chaudhry, Vinay; Goyal, Namita A; Alves, Christina; Salhi, Hayet; Wiesman, Janice F; Labeyrie, Celine; Robinson-Papp, Jessica; Cardoso, Márcio; Laura, Matilde; Ruzhansky, Katherine; Cortese, Andrea; Brannagan, Thomas H; Khoury, Julie; Khella, Sami; Waddington-Cruz, Márcia; Ferreira, João; Wang, Annabel K; Pinto, Marcus V; Ayache, Samar S; Benson, Merrill D; Berk, John L; Coelho, Teresa; Polydefkis, Michael; Gorevic, Peter; Adams, David H; Plante-Bordeneuve, Violaine; Whelan, Carol; Merlini, Giampaolo; Heitner, Stephen; Drachman, Brian M; Conceição, Isabel; Klein, Christopher J; Gertz, Morie A; Ackermann, Elizabeth J; Hughes, Steven G; Mauermann, Michelle L; Bergemann, Rito; Lodermeier, Karen A; Davies, Jenny L; Carter, Rickey E; Litchy, William J.
Affiliation
  • Dyck PJ; Department of Neurology, Mayo Clinic, 200 First Street SW, Rochester, Minnesota, 55905, USA.
  • Kincaid JC; Indiana University, IU Health, Indianapolis, Indiana, USA.
  • Dyck PJB; Department of Neurology, Mayo Clinic, 200 First Street SW, Rochester, Minnesota, 55905, USA.
  • Chaudhry V; Johns Hopkins University School of Medicine, Baltimore, Maryland, USA.
  • Goyal NA; University of California Irvine, Irvine, California, USA.
  • Alves C; Hospital Santo António, Centro Hospitalar Porto, Porto, Portugal.
  • Salhi H; Hôpitaux Universitaires Henri Mondor, Créteil, France.
  • Wiesman JF; Boston Medical Center, Boston, Massachusetts, USA.
  • Labeyrie C; CHU Bicêtre, French Reference Center for FAP (NNERF), Le Kremlin Bicêtre, France.
  • Robinson-Papp J; Icahn School of Medicine at Mount Sinai, New York, New York, USA.
  • Cardoso M; Hospital Santo António, Centro Hospitalar Porto, Porto, Portugal.
  • Laura M; National Hospital for Neurology and Neurosurgery, London, United Kingdom.
  • Ruzhansky K; Medical University of South Carolina, Charleston, South Carolina, USA.
  • Cortese A; C. Mondino National Neurological Institute, Pavia, Italy.
  • Brannagan TH; Columbia University, New York, New York, USA.
  • Khoury J; Oregon Health & Science University, Portland, Oregon, USA.
  • Khella S; Penn Presbyterian Medical Center, Philadelphia, Pennsylvania, USA.
  • Waddington-Cruz M; Clementino Fraga Filho University Hospital, Federal University of Rio de Janerio, Rio de Janerio, Brazil.
  • Ferreira J; New University of Lisbon, Lisbon, Portugal.
  • Wang AK; University of California-Irvine, Orange, California, USA.
  • Pinto MV; Clementino Fraga Filho University Hospital, Federal University of Rio de Janerio, Rio de Janerio, Brazil.
  • Ayache SS; Hôpitaux Universitaires Henri Mondor, Créteil, France.
  • Benson MD; Indiana University School of Medicine, Indianapolis, Indiana, USA.
  • Berk JL; Boston University School of Medicine, Boston, Massachusetts, USA.
  • Coelho T; Hospital Santo António, Centro Hospitalar Porto, Porto, Portugal.
  • Polydefkis M; Johns Hopkins University School of Medicine, Baltimore, Maryland, USA.
  • Gorevic P; Icahn School of Medicine at Mount Sinai, New York, New York, USA.
  • Adams DH; CHU Bicêtre, French Reference Center for FAP (NNERF), Le Kremlin Bicêtre, France.
  • Plante-Bordeneuve V; Hôpitaux Universitaires Henri Mondor, Créteil, France.
  • Whelan C; National Hospital for Neurology and Neurosurgery, London, United Kingdom.
  • Merlini G; Foundation IRCCS Policlinico San Matteo, University of Pavia, Italy.
  • Heitner S; Oregon Health & Science University, Portland, Oregon, USA.
  • Drachman BM; Penn Presbyterian Medical Center, Philadelphia, Pennsylvania, USA.
  • Conceição I; New University of Lisbon, Lisbon, Portugal.
  • Klein CJ; Department of Neurology, Mayo Clinic, 200 First Street SW, Rochester, Minnesota, 55905, USA.
  • Gertz MA; Department of Neurology, Mayo Clinic, 200 First Street SW, Rochester, Minnesota, 55905, USA.
  • Ackermann EJ; Ionis Pharmaceuticals, Inc, Carlsbad, California, USA.
  • Hughes SG; Ionis Pharmaceuticals, Inc, Carlsbad, California, USA.
  • Mauermann ML; Department of Neurology, Mayo Clinic, 200 First Street SW, Rochester, Minnesota, 55905, USA.
  • Bergemann R; GlaxoSmithKline, Middlesex, United Kingdom.
  • Lodermeier KA; Department of Neurology, Mayo Clinic, 200 First Street SW, Rochester, Minnesota, 55905, USA.
  • Davies JL; Department of Neurology, Mayo Clinic, 200 First Street SW, Rochester, Minnesota, 55905, USA.
  • Carter RE; Department of Neurology, Mayo Clinic, 200 First Street SW, Rochester, Minnesota, 55905, USA.
  • Litchy WJ; Department of Neurology, Mayo Clinic, 200 First Street SW, Rochester, Minnesota, 55905, USA.
Muscle Nerve ; 56(5): 901-911, 2017 Nov.
Article in En | MEDLINE | ID: mdl-28063170

Full text: 1 Collection: 01-internacional Database: MEDLINE Main subject: Oligonucleotides / Severity of Illness Index / Amyloid Neuropathies, Familial / Diagnostic Techniques, Neurological / Neurologists Type of study: Clinical_trials / Diagnostic_studies / Etiology_studies / Incidence_studies / Observational_studies / Risk_factors_studies Limits: Adult / Aged / Aged80 / Female / Humans / Male / Middle aged Language: En Journal: Muscle Nerve Year: 2017 Type: Article Affiliation country: United States

Full text: 1 Collection: 01-internacional Database: MEDLINE Main subject: Oligonucleotides / Severity of Illness Index / Amyloid Neuropathies, Familial / Diagnostic Techniques, Neurological / Neurologists Type of study: Clinical_trials / Diagnostic_studies / Etiology_studies / Incidence_studies / Observational_studies / Risk_factors_studies Limits: Adult / Aged / Aged80 / Female / Humans / Male / Middle aged Language: En Journal: Muscle Nerve Year: 2017 Type: Article Affiliation country: United States