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TRIAMF: A New Method for Delivery of Cas9 Ribonucleoprotein Complex to Human Hematopoietic Stem Cells.
Yen, Jonathan; Fiorino, Michael; Liu, Yi; Paula, Steve; Clarkson, Scott; Quinn, Lisa; Tschantz, William R; Klock, Heath; Guo, Ning; Russ, Carsten; Yu, Vionnie W C; Mickanin, Craig; Stevenson, Susan C; Lee, Cameron; Yang, Yi.
Affiliation
  • Yen J; Chemical Biology and Therapeutics, Novartis Institutes for BioMedical Research, Cambridge, Massachusetts, USA.
  • Fiorino M; NIBR Informatics, Novartis Institutes for BioMedical Research, Cambridge, Massachusetts, USA.
  • Liu Y; Chemical Biology and Therapeutics, Novartis Institutes for BioMedical Research, Cambridge, Massachusetts, USA.
  • Paula S; Chemical Biology and Therapeutics, Novartis Institutes for BioMedical Research, Cambridge, Massachusetts, USA.
  • Clarkson S; Chemical Biology and Therapeutics, Novartis Institutes for BioMedical Research, Cambridge, Massachusetts, USA.
  • Quinn L; Biotherapeutic and Analytical Tech, Novartis Institutes for BioMedical Research, Cambridge, Massachusetts, USA.
  • Tschantz WR; Biotherapeutic and Analytical Tech, Novartis Institutes for BioMedical Research, Cambridge, Massachusetts, USA.
  • Klock H; Biotherapeutics & Biotechnology, The Genomics Institute of the Novartis Research Foundation, La Jolla, California, USA.
  • Guo N; Chemical Biology and Therapeutics, Novartis Institutes for BioMedical Research, Cambridge, Massachusetts, USA.
  • Russ C; Chemical Biology and Therapeutics, Novartis Institutes for BioMedical Research, Cambridge, Massachusetts, USA.
  • Yu VWC; Chemical Biology and Therapeutics, Novartis Institutes for BioMedical Research, Cambridge, Massachusetts, USA.
  • Mickanin C; Chemical Biology and Therapeutics, Novartis Institutes for BioMedical Research, Cambridge, Massachusetts, USA.
  • Stevenson SC; Chemical Biology and Therapeutics, Novartis Institutes for BioMedical Research, Cambridge, Massachusetts, USA.
  • Lee C; Global Discovery Chemistry, Novartis Institutes for BioMedical Research, Cambridge, Massachusetts, USA.
  • Yang Y; Chemical Biology and Therapeutics, Novartis Institutes for BioMedical Research, Cambridge, Massachusetts, USA. yi.yang@novartis.com.
Sci Rep ; 8(1): 16304, 2018 11 02.
Article in En | MEDLINE | ID: mdl-30389991

Full text: 1 Collection: 01-internacional Database: MEDLINE Main subject: Ribonucleoproteins / Fetal Hemoglobin / Hematopoietic Stem Cell Transplantation / Filtration / Gene Editing Limits: Animals / Female / Humans Language: En Journal: Sci Rep Year: 2018 Type: Article Affiliation country: United States

Full text: 1 Collection: 01-internacional Database: MEDLINE Main subject: Ribonucleoproteins / Fetal Hemoglobin / Hematopoietic Stem Cell Transplantation / Filtration / Gene Editing Limits: Animals / Female / Humans Language: En Journal: Sci Rep Year: 2018 Type: Article Affiliation country: United States