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Risk stratification integrating genetic data for factor VIII inhibitor development in patients with severe hemophilia A.
Bachelet, Delphine; Albert, Thilo; Mbogning, Cyprien; Hässler, Signe; Zhang, Yuan; Schultze-Strasser, Stephan; Repessé, Yohann; Rayes, Julie; Pavlova, Anna; Pezeshkpoor, Behnaz; Liphardt, Kerstin; Davidson, Julie E; Hincelin-Méry, Agnès; Dönnes, Pierre; Lacroix-Desmazes, Sébastien; Königs, Christoph; Oldenburg, Johannes; Broët, Philippe.
Affiliation
  • Bachelet D; CESP, INSERM UMR 1018, Faculty of Medicine, Paris-Sud University, UVSQ, Paris-Saclay University, Villejuif, France.
  • Albert T; Institute of Experimental Haematology and Transfusion Medicine, University Clinic Bonn, Bonn, Germany.
  • Mbogning C; CESP, INSERM UMR 1018, Faculty of Medicine, Paris-Sud University, UVSQ, Paris-Saclay University, Villejuif, France.
  • Hässler S; CESP, INSERM UMR 1018, Faculty of Medicine, Paris-Sud University, UVSQ, Paris-Saclay University, Villejuif, France.
  • Zhang Y; CESP, INSERM UMR 1018, Faculty of Medicine, Paris-Sud University, UVSQ, Paris-Saclay University, Villejuif, France.
  • Schultze-Strasser S; University Hospital Frankfurt, Goethe University, Department of Pediatrics, Molecular Haemostasis and Immunodeficiency, Frankfurt am Main, Germany.
  • Repessé Y; CHU Caen, Hématologie Biologique, Caen, Caen, France.
  • Rayes J; Sorbonne Universités, UPMC Univ Paris 06, INSERM, Université Paris Descartes, Sorbonne Paris Cité, UMR_S 1138, Centre de Recherche des Cordeliers, Paris, France.
  • Pavlova A; Institute of Experimental Haematology and Transfusion Medicine, University Clinic Bonn, Bonn, Germany.
  • Pezeshkpoor B; Institute of Experimental Haematology and Transfusion Medicine, University Clinic Bonn, Bonn, Germany.
  • Liphardt K; Institute of Experimental Haematology and Transfusion Medicine, University Clinic Bonn, Bonn, Germany.
  • Davidson JE; GlaxoSmithKline, Uxbridge, Middlesex, United Kingdom.
  • Hincelin-Méry A; Sanofi, Chilly-Mazarin, France.
  • Dönnes P; SciCross AB, Skövde, Sweden.
  • Lacroix-Desmazes S; Sorbonne Universités, UPMC Univ Paris 06, INSERM, Université Paris Descartes, Sorbonne Paris Cité, UMR_S 1138, Centre de Recherche des Cordeliers, Paris, France.
  • Königs C; University Hospital Frankfurt, Goethe University, Department of Pediatrics, Molecular Haemostasis and Immunodeficiency, Frankfurt am Main, Germany.
  • Oldenburg J; Institute of Experimental Haematology and Transfusion Medicine, University Clinic Bonn, Bonn, Germany.
  • Broët P; CESP, INSERM UMR 1018, Faculty of Medicine, Paris-Sud University, UVSQ, Paris-Saclay University, Villejuif, France.
PLoS One ; 14(6): e0218258, 2019.
Article in En | MEDLINE | ID: mdl-31194850

Full text: 1 Collection: 01-internacional Database: MEDLINE Main subject: Factor VIII / Risk Assessment / Hemophilia A Type of study: Etiology_studies / Observational_studies / Prognostic_studies / Risk_factors_studies Limits: Humans Country/Region as subject: Europa Language: En Journal: PLoS One Journal subject: CIENCIA / MEDICINA Year: 2019 Type: Article Affiliation country: France

Full text: 1 Collection: 01-internacional Database: MEDLINE Main subject: Factor VIII / Risk Assessment / Hemophilia A Type of study: Etiology_studies / Observational_studies / Prognostic_studies / Risk_factors_studies Limits: Humans Country/Region as subject: Europa Language: En Journal: PLoS One Journal subject: CIENCIA / MEDICINA Year: 2019 Type: Article Affiliation country: France