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Expanded circulating hematopoietic stem/progenitor cells as novel cell source for the treatment of TCIRG1 osteopetrosis.
Capo, Valentina; Penna, Sara; Merelli, Ivan; Barcella, Matteo; Scala, Serena; Basso-Ricci, Luca; Draghici, Elena; Palagano, Eleonora; Zonari, Erika; Desantis, Giacomo; Uva, Paolo; Cusano, Roberto; Sergi Sergi, Lucia; Crisafulli, Laura; Moshous, Despina; Stepensky, Polina; Drabko, Katarzyna; Kaya, Zühre; Unal, Ekrem; Gezdirici, Alper; Menna, Giuseppe; Serafini, Marta; Aiuti, Alessandro; Locatelli, Silvia Laura; Carlo-Stella, Carmelo; Schulz, Ansgar S; Ficara, Francesca; Sobacchi, Cristina; Gentner, Bernhard; Villa, Anna.
Affiliation
  • Capo V; San Raffaele Telethon Institute for Gene Therapy (SR-Tiget), IRCCS San Raffaele Scientific Institute.
  • Penna S; San Raffaele Telethon Institute for Gene Therapy (SR-Tiget), IRCCS San Raffaele Scientific Institute.
  • Merelli I; Institute for Biomedical Technologies, National Research Council, Serrate, Italy.
  • Barcella M; San Raffaele Telethon Institute for Gene Therapy (SR-Tiget), IRCCS San Raffaele Scientific Institute.
  • Scala S; San Raffaele Telethon Institute for Gene Therapy (SR-Tiget), IRCCS San Raffaele Scientific Institute.
  • Basso-Ricci L; San Raffaele Telethon Institute for Gene Therapy (SR-Tiget), IRCCS San Raffaele Scientific Institute.
  • Draghici E; San Raffaele Telethon Institute for Gene Therapy (SR-Tiget), IRCCS San Raffaele Scientific Institute.
  • Palagano E; CNR-IRGB, Milan Unit and Humanitas Clinical and Research Center - IRCCS, Milano, Italy.
  • Zonari E; San Raffaele Telethon Institute for Gene Therapy (SR-Tiget), IRCCS San Raffaele Scientific Institute.
  • Desantis G; San Raffaele Telethon Institute for Gene Therapy (SR-Tiget), IRCCS San Raffaele Scientific Institute.
  • Uva P; CRS4, Science and Technology Park Polaris, Pula, Italy.
  • Cusano R; CRS4, Science and Technology Park Polaris, Pula, Italy.
  • Sergi Sergi L; San Raffaele Telethon Institute for Gene Therapy (SR-Tiget), IRCCS San Raffaele Scientific Institute.
  • Crisafulli L; CNR-IRGB, Milan Unit and Humanitas Clinical and Research Center - IRCCS, Milano, Italy.
  • Moshous D; Immunologie, Hematologie et Rhumatologie Pediatriques, Hopital Necker-Enfants Malades, Paris, France.
  • Stepensky P; Dept. of Bone Marrow Transplantation and Cancer Immunotherapy, Hadassah University Hospital, Jerusalem.
  • Drabko K; Medical University of Lublin.
  • Kaya Z; Department of Pediatric Hematology, Gazi University, School of Medicine, Ankara, Turkey.
  • Unal E; Erciyes University, Pediatric Hematology Oncology, Kayseri.
  • Gezdirici A; Istanbul Health Science University, Kanuni Sultan Suleyman Training and Research Hospital.
  • Menna G; Hemato-Oncology Unit, Department of Oncology, Pausilipon Hospital, Napoli, italy.
  • Serafini M; DIMET, University of Milano-Bicocca, Monza, Italy.
  • Aiuti A; San Raffaele Telethon Institute for Gene Therapy (SR-Tiget), IRCCS San Raffaele Scientific Institute.
  • Locatelli SL; Humanitas Cancer Center, Humanitas Clinical and Research Center, Rozzano.
  • Carlo-Stella C; Humanitas Cancer Center, Humanitas Clinical and Research Center, Rozzano, Italy.
  • Schulz AS; Department of Pediatrics and Adolescent Medicine, Ulm University Medical Center, Ulm.
  • Ficara F; CNR-IRGB, Milan Unit and Humanitas Clinical and Research Center - IRCCS, Milano.
  • Sobacchi C; CNR-IRGB, Milan Unit and Humanitas Clinical and Research Center - IRCCS, Milano.
  • Gentner B; San Raffaele Telethon Institute for Gene Therapy (SR-Tiget), IRCCS San Raffaele Scientific Institute.
  • Villa A; San Raffaele Telethon Institute for Gene Therapy (SR-Tiget), IRCCS San Raffaele Scientific Institute.
Haematologica ; 106(1): 74-86, 2021 01 01.
Article in En | MEDLINE | ID: mdl-31949009

Full text: 1 Collection: 01-internacional Database: MEDLINE Main subject: Osteopetrosis / Hematopoietic Stem Cell Transplantation / Vacuolar Proton-Translocating ATPases Type of study: Guideline Limits: Humans Language: En Journal: Haematologica Year: 2021 Type: Article

Full text: 1 Collection: 01-internacional Database: MEDLINE Main subject: Osteopetrosis / Hematopoietic Stem Cell Transplantation / Vacuolar Proton-Translocating ATPases Type of study: Guideline Limits: Humans Language: En Journal: Haematologica Year: 2021 Type: Article