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Nusinersen treatment in adults with severe spinal muscular atrophy: A real-life retrospective observational cohort study.
Lefeuvre, C; Brisset, M; Sarlon, M; Petit, N; Orlikowski, D; Clair, B; Thiry, T; Carlier, R-Y; Prigent, H; Nicolas, G; Annane, D; Laforet, P; Pouplin, S.
Affiliation
  • Lefeuvre C; Neurology department, Raymond-Poincaré university hospital, AP-HP, Garches, France; Nord-Est-Île-de-France neuromuscular reference center, FHU PHENIX, France; Université Paris-Saclay, UVSQ, ERPHAN, 78000 Versailles, France. Electronic address: claire.lefeuvre@aphp.fr.
  • Brisset M; Neurology department, Raymond-Poincaré university hospital, AP-HP, Garches, France; Nord-Est-Île-de-France neuromuscular reference center, FHU PHENIX, France; Université Paris-Saclay, UVSQ, ERPHAN, 78000 Versailles, France.
  • Sarlon M; New Technologies Platform, Raymond-Poincaré hospital, AP-HP, Garches, France; Université Paris-Saclay, UVSQ, ERPHAN, 78000 Versailles, France.
  • Petit N; Neurology department, Raymond-Poincaré university hospital, AP-HP, Garches, France; Université Paris-Saclay, UVSQ, ERPHAN, 78000 Versailles, France.
  • Orlikowski D; Critical care medical department, Raymond-Poincaré hospital, AP-HP, Garches, France; CIC 1429 AP-HP INSERM, université Versailles-Saint-Quentin-en-Yvelines, Paris-Saclay, France; Université Paris-Saclay, UVSQ, ERPHAN, 78000 Versailles, France.
  • Clair B; Critical care medical department, Raymond-Poincaré hospital, AP-HP, Garches, France; Université Paris-Saclay, UVSQ, ERPHAN, 78000 Versailles, France.
  • Thiry T; Diagnostic and interventional medical imaging department, Raymond-Poincaré hospital, DMU smart imaging, GH université Paris-Saclay, AP-HP, Garches, France; Université Paris-Saclay, UVSQ, ERPHAN, 78000 Versailles, France.
  • Carlier RY; U 1179 INSERM, université Versailles-Saint-Quentin-en-Yvelines, Paris-Saclay, France; Diagnostic and interventional medical imaging department, Raymond-Poincaré hospital, DMU smart imaging, GH université Paris-Saclay, AP-HP, Garches, France; Université Paris-Saclay, UVSQ, ERPHAN, 78000 Versailles, F
  • Prigent H; Nord-Est-Île-de-France neuromuscular reference center, FHU PHENIX, France; Université Paris-Saclay, UVSQ, ERPHAN, 78000 Versailles, France; Physiology department, Raymond-Poincaré university hospital, AP-HP, Garches, France.
  • Nicolas G; Neurology department, Raymond-Poincaré university hospital, AP-HP, Garches, France; Nord-Est-Île-de-France neuromuscular reference center, FHU PHENIX, France; U 1179 INSERM, université Versailles-Saint-Quentin-en-Yvelines, Paris-Saclay, France; Université Paris-Saclay, UVSQ, ERPHAN, 78000 Versailles
  • Annane D; Critical care medical department, Raymond-Poincaré hospital, AP-HP, Garches, France; Université Paris-Saclay, UVSQ, ERPHAN, 78000 Versailles, France.
  • Laforet P; Neurology department, Raymond-Poincaré university hospital, AP-HP, Garches, France; Nord-Est-Île-de-France neuromuscular reference center, FHU PHENIX, France; U 1179 INSERM, université Versailles-Saint-Quentin-en-Yvelines, Paris-Saclay, France; Université Paris-Saclay, UVSQ, ERPHAN, 78000 Versailles
  • Pouplin S; New Technologies Platform, Raymond-Poincaré hospital, AP-HP, Garches, France; U 1179 INSERM, université Versailles-Saint-Quentin-en-Yvelines, Paris-Saclay, France; Université Paris-Saclay, UVSQ, ERPHAN, 78000 Versailles, France.
Rev Neurol (Paris) ; 178(3): 234-240, 2022 Mar.
Article in En | MEDLINE | ID: mdl-35000792

Full text: 1 Collection: 01-internacional Database: MEDLINE Main subject: Muscular Atrophy, Spinal / Spinal Muscular Atrophies of Childhood / Neurodegenerative Diseases Type of study: Etiology_studies / Observational_studies / Prognostic_studies Limits: Adult / Humans Country/Region as subject: America do norte Language: En Journal: Rev Neurol (Paris) Year: 2022 Type: Article

Full text: 1 Collection: 01-internacional Database: MEDLINE Main subject: Muscular Atrophy, Spinal / Spinal Muscular Atrophies of Childhood / Neurodegenerative Diseases Type of study: Etiology_studies / Observational_studies / Prognostic_studies Limits: Adult / Humans Country/Region as subject: America do norte Language: En Journal: Rev Neurol (Paris) Year: 2022 Type: Article