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Real-life experience with inotersen in hereditary transthyretin amyloidosis with late-onset phenotype: Data from an early-access program in Italy.
Luigetti, Marco; Antonini, Giovanni; Di Paolantonio, Andrea; Gentile, Luca; Grandis, Marina; Leonardi, Luca; Lozza, Alessandro; Manganelli, Fiore; Mazzeo, Anna; Mussinelli, Roberta; My, Filomena; Obici, Laura; Maria Pennisi, Elena; Romozzi, Marina; Russo, Massimo; Sabatelli, Mario; Salvalaggio, Alessandro; Tagliapietra, Matteo; Tozza, Stefano.
Affiliation
  • Luigetti M; Fondazione Policlinico Universitario Agostino Gemelli IRCCS UOC Neurologia, Rome, Italy.
  • Antonini G; Department of Neuroscience, Catholic University of the Sacred Heart, Rome, Italy.
  • Di Paolantonio A; Department of Neurosciences, Mental Health and Sensory Organs, Faculty of Medicine and Psychology, Sant'Andrea Hospital, Sapienza University of Rome, Rome, Italy.
  • Gentile L; Department of Neuroscience, Catholic University of the Sacred Heart, Rome, Italy.
  • Grandis M; Unit of Neurology and Neuromuscular Diseases, Department of Clinical and Experimental Medicine, University of Messina, Messina, Italy.
  • Leonardi L; Department of Neurosciences, Rehabilitation, Ophthalmology, Genetics and Maternal Infantile Sciences, University of Genova, Genoa, Italy.
  • Lozza A; San Martino Polyclinic Hospital, Scientific Institute for Research and Health Care, Genoa, Italy.
  • Manganelli F; Department of Neurosciences, Mental Health and Sensory Organs, Faculty of Medicine and Psychology, Sant'Andrea Hospital, Sapienza University of Rome, Rome, Italy.
  • Mazzeo A; Amyloidosis Research and Treatment Center, San Matteo Polyclinic Foundation, Scientific Institute for Research and Health Care, Pavia, Italy.
  • Mussinelli R; Department of Neuroscience, Reproductive and Odontostomatological Science, University of Naples "Federico II", Naples, Italy.
  • My F; Unit of Neurology and Neuromuscular Diseases, Department of Clinical and Experimental Medicine, University of Messina, Messina, Italy.
  • Obici L; Amyloidosis Research and Treatment Center, San Matteo Polyclinic Foundation, Scientific Institute for Research and Health Care, Pavia, Italy.
  • Maria Pennisi E; UOC Neurologia Vito Fazzi Hospital, Lecce, Italy.
  • Romozzi M; Amyloidosis Research and Treatment Center, San Matteo Polyclinic Foundation, Scientific Institute for Research and Health Care, Pavia, Italy.
  • Russo M; Neuromuscular and Rare Neurological Diseases-Neurology Unit, San Filippo Neri Hospital, Rome, Italy.
  • Sabatelli M; Fondazione Policlinico Universitario Agostino Gemelli IRCCS UOC Neurologia, Rome, Italy.
  • Salvalaggio A; Department of Neuroscience, Catholic University of the Sacred Heart, Rome, Italy.
  • Tagliapietra M; Unit of Neurology and Neuromuscular Diseases, Department of Clinical and Experimental Medicine, University of Messina, Messina, Italy.
  • Tozza S; Centro Clinico NEMO Fondazione Policlinico Universitario A. Gemelli IRCCS, Rome, Italy.
Eur J Neurol ; 29(7): 2148-2155, 2022 07.
Article in En | MEDLINE | ID: mdl-35289020

Full text: 1 Collection: 01-internacional Database: MEDLINE Main subject: Thrombocytopenia / Amyloid Neuropathies, Familial Type of study: Observational_studies / Risk_factors_studies Limits: Humans Country/Region as subject: Europa Language: En Journal: Eur J Neurol Journal subject: NEUROLOGIA Year: 2022 Type: Article Affiliation country: Italy

Full text: 1 Collection: 01-internacional Database: MEDLINE Main subject: Thrombocytopenia / Amyloid Neuropathies, Familial Type of study: Observational_studies / Risk_factors_studies Limits: Humans Country/Region as subject: Europa Language: En Journal: Eur J Neurol Journal subject: NEUROLOGIA Year: 2022 Type: Article Affiliation country: Italy