The Amyloid Inhibitor CLR01 Relieves Autophagy and Ameliorates Neuropathology in a Severe Lysosomal Storage Disease.

Monaco, Antonio; Maffia, Veronica; Sorrentino, Nicolina Cristina; Sambri, Irene; Ezhova, Yulia; Giuliano, Teresa; Cacace, Vincenzo; Nusco, Edoardo; De Risi, Maria; De Leonibus, Elvira; Schrader, Thomas; Klärner, Frank-Gerrit; Bitan, Gal; Fraldi, Alessandro

Monaco, Antonio; Maffia, Veronica; Sorrentino, Nicolina Cristina; Sambri, Irene; Ezhova, Yulia; Giuliano, Teresa; Cacace, Vincenzo; Nusco, Edoardo; De Risi, Maria; De Leonibus, Elvira; Schrader, Thomas; Klärner, Frank-Gerrit; Bitan, Gal; Fraldi, Alessandro.

Mol Ther ; 30(11): 3499, 2022 Nov 02.

Article in En | MEDLINE | ID: mdl-36261045

Fulltext

https://www.ncbi.nlm.nih.gov/pmc/articles/PMC9637752
https://dx.doi.org/10.1016/j.ymthe.2022.10.001

XML

PubMed Links

Search on Google

Full text: 1 Collection: 01-internacional Database: MEDLINE Language: En Journal: Mol Ther Journal subject: BIOLOGIA MOLECULAR / TERAPEUTICA Year: 2022 Type: Article

Fulltext

https://www.ncbi.nlm.nih.gov/pmc/articles/PMC9637752
https://dx.doi.org/10.1016/j.ymthe.2022.10.001

XML

PubMed Links

Search on Google

Full text: 1 Collection: 01-internacional Database: MEDLINE Language: En Journal: Mol Ther Journal subject: BIOLOGIA MOLECULAR / TERAPEUTICA Year: 2022 Type: Article