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Enzyme replacement therapy delays pupillary light reflex deficits in a canine model of late infantile neuronal ceroid lipofuscinosis.
Whiting, Rebecca E H; Narfström, Kristina; Yao, Gang; Pearce, Jacqueline W; Coates, Joan R; Castaner, Leilani J; Jensen, Cheryl A; Dougherty, Brittanie N; Vuillemenot, Brian R; Kennedy, Derek; O'Neill, Charles A; Katz, Martin L.
Afiliación
  • Whiting RE; Department of Bioengineering, University of Missouri, Columbia, MO 65211, USA; Department of Veterinary Medicine and Surgery, University of Missouri, Columbia, MO 65211, USA.
  • Narfström K; Department of Veterinary Medicine and Surgery, University of Missouri, Columbia, MO 65211, USA.
  • Yao G; Department of Bioengineering, University of Missouri, Columbia, MO 65211, USA.
  • Pearce JW; Department of Veterinary Medicine and Surgery, University of Missouri, Columbia, MO 65211, USA.
  • Coates JR; Department of Veterinary Medicine and Surgery, University of Missouri, Columbia, MO 65211, USA.
  • Castaner LJ; Department of Ophthalmology, University of Missouri, Columbia, MO 65212, USA.
  • Jensen CA; Department of Ophthalmology, University of Missouri, Columbia, MO 65212, USA.
  • Dougherty BN; Department of Bioengineering, University of Missouri, Columbia, MO 65211, USA; Department of Ophthalmology, University of Missouri, Columbia, MO 65212, USA.
  • Vuillemenot BR; BioMarin Pharmaceutical Inc., Novato, CA 94949, USA.
  • Kennedy D; BioMarin Pharmaceutical Inc., Novato, CA 94949, USA.
  • O'Neill CA; BioMarin Pharmaceutical Inc., Novato, CA 94949, USA.
  • Katz ML; Department of Bioengineering, University of Missouri, Columbia, MO 65211, USA; Department of Ophthalmology, University of Missouri, Columbia, MO 65212, USA. Electronic address: katzm@health.missouri.edu.
Exp Eye Res ; 125: 164-72, 2014 Aug.
Article en En | MEDLINE | ID: mdl-24954537

Texto completo: 1 Colección: 01-internacional Banco de datos: MEDLINE Asunto principal: Reflejo Pupilar / Dipeptidil-Peptidasas y Tripeptidil-Peptidasas / Serina Proteasas / Terapia de Reemplazo Enzimático / Aminopeptidasas / Lipofuscinosis Ceroideas Neuronales Tipo de estudio: Prognostic_studies Límite: Animals Idioma: En Revista: Exp Eye Res Año: 2014 Tipo del documento: Article País de afiliación: Estados Unidos

Texto completo: 1 Colección: 01-internacional Banco de datos: MEDLINE Asunto principal: Reflejo Pupilar / Dipeptidil-Peptidasas y Tripeptidil-Peptidasas / Serina Proteasas / Terapia de Reemplazo Enzimático / Aminopeptidasas / Lipofuscinosis Ceroideas Neuronales Tipo de estudio: Prognostic_studies Límite: Animals Idioma: En Revista: Exp Eye Res Año: 2014 Tipo del documento: Article País de afiliación: Estados Unidos