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Combination Antisense Treatment for Destructive Exon Skipping of Myostatin and Open Reading Frame Rescue of Dystrophin in Neonatal mdx Mice.
Lu-Nguyen, Ngoc B; Jarmin, Susan A; Saleh, Amer F; Popplewell, Linda; Gait, Michael J; Dickson, George.
Afiliación
  • Lu-Nguyen NB; School of Biological Sciences, Royal Holloway, University of London, Surrey, UK.
  • Jarmin SA; School of Biological Sciences, Royal Holloway, University of London, Surrey, UK.
  • Saleh AF; Medical Research Council, Laboratory of Molecular Biology, Francis Crick Avenue, Cambridge Biomedical Campus, Cambridge, UK; Current address: AstraZeneca R&D, Discovery Safety, Drug Safety and Metabolism, Alderley Park, Macclesfield, UK.
  • Popplewell L; School of Biological Sciences, Royal Holloway, University of London, Surrey, UK.
  • Gait MJ; Medical Research Council, Laboratory of Molecular Biology, Francis Crick Avenue, Cambridge Biomedical Campus, Cambridge, UK.
  • Dickson G; School of Biological Sciences, Royal Holloway, University of London, Surrey, UK. Electronic address: G.Dickson@rhul.ac.uk.
Mol Ther ; 23(8): 1341-1348, 2015 Aug.
Article en En | MEDLINE | ID: mdl-25959011

Texto completo: 1 Colección: 01-internacional Banco de datos: MEDLINE Asunto principal: Exones / Distrofina / Oligonucleótidos Antisentido / Sistemas de Lectura Abierta / Miostatina Tipo de estudio: Prognostic_studies Límite: Animals Idioma: En Revista: Mol Ther Asunto de la revista: BIOLOGIA MOLECULAR / TERAPEUTICA Año: 2015 Tipo del documento: Article País de afiliación: Reino Unido

Texto completo: 1 Colección: 01-internacional Banco de datos: MEDLINE Asunto principal: Exones / Distrofina / Oligonucleótidos Antisentido / Sistemas de Lectura Abierta / Miostatina Tipo de estudio: Prognostic_studies Límite: Animals Idioma: En Revista: Mol Ther Asunto de la revista: BIOLOGIA MOLECULAR / TERAPEUTICA Año: 2015 Tipo del documento: Article País de afiliación: Reino Unido