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Generation of Human Induced Pluripotent Stem Cell-Derived Bona Fide Neural Stem Cells for Ex Vivo Gene Therapy of Metachromatic Leukodystrophy.
Meneghini, Vasco; Frati, Giacomo; Sala, Davide; De Cicco, Silvia; Luciani, Marco; Cavazzin, Chiara; Paulis, Marianna; Mentzen, Wieslawa; Morena, Francesco; Giannelli, Serena; Sanvito, Francesca; Villa, Anna; Bulfone, Alessandro; Broccoli, Vania; Martino, Sabata; Gritti, Angela.
Afiliación
  • Meneghini V; San Raffaele Telethon Institute for Gene Therapy, Division of Regenerative Medicine, Stem Cells and Gene Therapy, Istituto di Ricovero e Cura a Carattere Scientifico San Raffaele, Milan, Italy.
  • Frati G; San Raffaele Telethon Institute for Gene Therapy, Division of Regenerative Medicine, Stem Cells and Gene Therapy, Istituto di Ricovero e Cura a Carattere Scientifico San Raffaele, Milan, Italy.
  • Sala D; San Raffaele Telethon Institute for Gene Therapy, Division of Regenerative Medicine, Stem Cells and Gene Therapy, Istituto di Ricovero e Cura a Carattere Scientifico San Raffaele, Milan, Italy.
  • De Cicco S; San Raffaele Telethon Institute for Gene Therapy, Division of Regenerative Medicine, Stem Cells and Gene Therapy, Istituto di Ricovero e Cura a Carattere Scientifico San Raffaele, Milan, Italy.
  • Luciani M; San Raffaele Telethon Institute for Gene Therapy, Division of Regenerative Medicine, Stem Cells and Gene Therapy, Istituto di Ricovero e Cura a Carattere Scientifico San Raffaele, Milan, Italy.
  • Cavazzin C; San Raffaele Telethon Institute for Gene Therapy, Division of Regenerative Medicine, Stem Cells and Gene Therapy, Istituto di Ricovero e Cura a Carattere Scientifico San Raffaele, Milan, Italy.
  • Paulis M; National Research Council, Milan, Italy.
  • Mentzen W; Humanitas Clinical and Research Center, Rozzano, Italy.
  • Morena F; BioFlag Ltd., Pula, Cagliari, Italy.
  • Giannelli S; Biochemistry and Molecular Biology Unit, Department of Chemistry, Biology and Biotechnologies, University of Perugia, Perugia, Italy.
  • Sanvito F; Division of Neuroscience, Istituto di Ricovero e Cura a Carattere Scientifico San Raffaele, Milan, Italy.
  • Villa A; Anatomy and Histopathology Department, Istituto di Ricovero e Cura a Carattere Scientifico San Raffaele, Milan, Italy.
  • Bulfone A; San Raffaele Telethon Institute for Gene Therapy, Division of Regenerative Medicine, Stem Cells and Gene Therapy, Istituto di Ricovero e Cura a Carattere Scientifico San Raffaele, Milan, Italy.
  • Broccoli V; National Research Council, Milan, Italy.
  • Martino S; Humanitas Clinical and Research Center, Rozzano, Italy.
  • Gritti A; BioFlag Ltd., Pula, Cagliari, Italy.
Stem Cells Transl Med ; 6(2): 352-368, 2017 02.
Article en En | MEDLINE | ID: mdl-28191778

Texto completo: 1 Colección: 01-internacional Banco de datos: MEDLINE Asunto principal: Terapia Genética / Cerebrósido Sulfatasa / Trasplante de Células Madre / Reprogramación Celular / Células Madre Pluripotentes Inducidas / Células-Madre Neurales / Técnicas de Reprogramación Celular / Leucodistrofia Metacromática Tipo de estudio: Guideline / Prognostic_studies Límite: Animals / Humans Idioma: En Revista: Stem Cells Transl Med Año: 2017 Tipo del documento: Article País de afiliación: Italia

Texto completo: 1 Colección: 01-internacional Banco de datos: MEDLINE Asunto principal: Terapia Genética / Cerebrósido Sulfatasa / Trasplante de Células Madre / Reprogramación Celular / Células Madre Pluripotentes Inducidas / Células-Madre Neurales / Técnicas de Reprogramación Celular / Leucodistrofia Metacromática Tipo de estudio: Guideline / Prognostic_studies Límite: Animals / Humans Idioma: En Revista: Stem Cells Transl Med Año: 2017 Tipo del documento: Article País de afiliación: Italia