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Duchenne Regulatory Science Consortium Meeting on Disease Progression Modeling for Duchenne Muscular Dystrophy.
Larkindale, Jane; Abresch, Richard; Aviles, Enrique; Bronson, Abby; Chin, Janice; Furlong, Pat; Gordish-Dressman, Heather; Habeeb-Louks, Elizabeth; Henricson, Erik; Kroger, Hans; Lynn, Charles; Lynn, Stephen; Martin, Dana; Nuckolls, Glen; Rooney, William; Romero, Klaus; Sweeney, Lee; Vandenborne, Krista; Walter, Glenn; Wolff, Jodi; Wong, Brenda; McDonald, Craig M; Duchenne Regulatory Science Consortium Imaging-Dmd Consortium And The Cinrg Investigators, Members Of The.
Afiliación
  • Abresch R; Department of Physical Medicine and Rehabilitation, University of California, Sacramento, California, USA.
  • Aviles E; Duchenne Regulatory Science Consortium, Critical Path Institute, Tucson, Arizona, USA.
  • Bronson A; Parent Project Muscular Dystrophy, Hackensack, New Jersey, USA.
  • Chin J; Pfizer, Rare Disease Research Unit, Cambridge, Massachusetts, USA.
  • Furlong P; Parent Project Muscular Dystrophy, Hackensack, New Jersey, USA.
  • Gordish-Dressman H; Children's National Medical Center, Research Center for Genetic Medicine, Washington, DC, USA.
  • Habeeb-Louks E; Parent Project Muscular Dystrophy, Hackensack, New Jersey, USA.
  • Henricson E; University of California Davis Medical Center, Department of Physical Medicine and Rehabilitation, Sacramento, California, USA.
  • Kroger H; PTC Therapeutics, South Plainfield, New Jersey, USA.
  • Lynn C; Duchenne Regulatory Science Consortium, Critical Path Institute, Tucson, Arizona, USA.
  • Lynn S; Stephen Lynn, Newcastle University, Newcastle upon Tyne, UK.
  • Martin D; Sarepta Therapeutics, Medical Affairs & Patient Advocacy, Cambridge, Massachusetts, USA.
  • Nuckolls G; NINDS, National Institute of Health, Washington DC, USA.
  • Rooney W; Advanced Imaging Research Center, Oregon Health & Science University, Portland, Oregon, USA.
  • Romero K; Duchenne Regulatory Science Consortium, Critical Path Institute, Tucson, Arizona, USA.
  • Sweeney L; Department of Pharmacology and Therapeutics, University of Florida, Gainesville, Florida, USA.
  • Vandenborne K; Department of Physical Therapy, University of Florida, Gainesville, Florida, USA.
  • Walter G; Department of Physiology and Functional Genomics, University of Florida, Gainesville, Florida, USA.
  • Wolff J; Santhera Pharmaceuticals, Tucson, Arizona, USA.
  • Wong B; Division of Pediatric Neurology, Cincinnati Children's Hospital Medical Center, Cincinnati, Ohio, USA.
  • McDonald CM; Department of Physical Medicine and Rehabilitation, University of California, Sacramento, California, USA.
PLoS Curr ; 92017 Jan 12.
Article en En | MEDLINE | ID: mdl-28228973

Texto completo: 1 Colección: 01-internacional Banco de datos: MEDLINE Tipo de estudio: Guideline Idioma: En Revista: PLoS Curr Año: 2017 Tipo del documento: Article

Texto completo: 1 Colección: 01-internacional Banco de datos: MEDLINE Tipo de estudio: Guideline Idioma: En Revista: PLoS Curr Año: 2017 Tipo del documento: Article