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CRISPR/Cas9-based genetic correction for recessive dystrophic epidermolysis bullosa.
Webber, Beau R; Osborn, Mark J; McElroy, Amber N; Twaroski, Kirk; Lonetree, Cara-Lin; DeFeo, Anthony P; Xia, Lily; Eide, Cindy; Lees, Christopher J; McElmurry, Ron T; Riddle, Megan J; Kim, Chong Jai; Patel, Dharmeshkumar D; Blazar, Bruce R; Tolar, Jakub.
Afiliación
  • Webber BR; Department of Pediatrics, Division of Blood and Marrow Transplantation, University of Minnesota, Minneapolis, MN, USA.
  • Osborn MJ; Department of Pediatrics, Division of Blood and Marrow Transplantation, University of Minnesota, Minneapolis, MN, USA.
  • McElroy AN; Stem Cell Institute, University of Minnesota, Minneapolis, MN, USA.
  • Twaroski K; Center for Genome Engineering, University of Minnesota, Minneapolis, MN, USA.
  • Lonetree CL; Asan-Minnesota Institute for Innovating Transplantation, Seoul, Republic of Korea.
  • DeFeo AP; Department of Pediatrics, Division of Blood and Marrow Transplantation, University of Minnesota, Minneapolis, MN, USA.
  • Xia L; Department of Pediatrics, Division of Blood and Marrow Transplantation, University of Minnesota, Minneapolis, MN, USA.
  • Eide C; Department of Pediatrics, Division of Blood and Marrow Transplantation, University of Minnesota, Minneapolis, MN, USA.
  • Lees CJ; Department of Pediatrics, Division of Blood and Marrow Transplantation, University of Minnesota, Minneapolis, MN, USA.
  • McElmurry RT; Department of Pediatrics, Division of Blood and Marrow Transplantation, University of Minnesota, Minneapolis, MN, USA.
  • Riddle MJ; Department of Pediatrics, Division of Blood and Marrow Transplantation, University of Minnesota, Minneapolis, MN, USA.
  • Kim CJ; Department of Pediatrics, Division of Blood and Marrow Transplantation, University of Minnesota, Minneapolis, MN, USA.
  • Patel DD; Department of Pediatrics, Division of Blood and Marrow Transplantation, University of Minnesota, Minneapolis, MN, USA.
  • Blazar BR; Department of Pediatrics, Division of Blood and Marrow Transplantation, University of Minnesota, Minneapolis, MN, USA.
  • Tolar J; Asan-Minnesota Institute for Innovating Transplantation, Seoul, Republic of Korea.
Article en En | MEDLINE | ID: mdl-28250968

Texto completo: 1 Colección: 01-internacional Banco de datos: MEDLINE Idioma: En Revista: NPJ Regen Med Año: 2016 Tipo del documento: Article País de afiliación: Estados Unidos

Texto completo: 1 Colección: 01-internacional Banco de datos: MEDLINE Idioma: En Revista: NPJ Regen Med Año: 2016 Tipo del documento: Article País de afiliación: Estados Unidos