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AAVrh10 Gene Therapy Ameliorates Central and Peripheral Nervous System Disease in Canine Globoid Cell Leukodystrophy (Krabbe Disease).
Bradbury, Allison M; Rafi, Mohammed A; Bagel, Jessica H; Brisson, Becky K; Marshall, Michael S; Pesayco Salvador, Jill; Jiang, Xuntain; Swain, Gary P; Prociuk, Maria L; ODonnell, Patricia A; Fitzgerald, Caitlin; Ory, Daniel S; Bongarzone, Ernesto R; Shelton, G Diane; Wenger, David A; Vite, Charles H.
Afiliación
  • Bradbury AM; 1 Department of Clinical Sciences and Advanced Medicine, School of Veterinary Medicine, University of Pennsylvania , Philadelphia, Pennsylvania.
  • Rafi MA; 2 Department of Neurology, Sidney Kimmel College of Medicine, Thomas Jefferson University , Philadelphia, Pennsylvania.
  • Bagel JH; 1 Department of Clinical Sciences and Advanced Medicine, School of Veterinary Medicine, University of Pennsylvania , Philadelphia, Pennsylvania.
  • Brisson BK; 1 Department of Clinical Sciences and Advanced Medicine, School of Veterinary Medicine, University of Pennsylvania , Philadelphia, Pennsylvania.
  • Marshall MS; 3 Department of Anatomy and Cell Biology, College of Medicine, University of Illinois , Chicago, Illinois.
  • Pesayco Salvador J; 4 Department of Pathology, School of Medicine, Comparative Neuromuscular Laboratory, University of California , San Diego, La Jolla, California.
  • Jiang X; 5 Diabetic Cardiovascular Disease Center, Washington University School of Medicine , St. Louis, Missouri.
  • Swain GP; 1 Department of Clinical Sciences and Advanced Medicine, School of Veterinary Medicine, University of Pennsylvania , Philadelphia, Pennsylvania.
  • Prociuk ML; 1 Department of Clinical Sciences and Advanced Medicine, School of Veterinary Medicine, University of Pennsylvania , Philadelphia, Pennsylvania.
  • ODonnell PA; 1 Department of Clinical Sciences and Advanced Medicine, School of Veterinary Medicine, University of Pennsylvania , Philadelphia, Pennsylvania.
  • Fitzgerald C; 1 Department of Clinical Sciences and Advanced Medicine, School of Veterinary Medicine, University of Pennsylvania , Philadelphia, Pennsylvania.
  • Ory DS; 5 Diabetic Cardiovascular Disease Center, Washington University School of Medicine , St. Louis, Missouri.
  • Bongarzone ER; 3 Department of Anatomy and Cell Biology, College of Medicine, University of Illinois , Chicago, Illinois.
  • Shelton GD; 6 Departamento de Química Biologica, Facultad de Farmacia y Bioquímica, Universidad de Buenos Aires , Argentina .
  • Wenger DA; 4 Department of Pathology, School of Medicine, Comparative Neuromuscular Laboratory, University of California , San Diego, La Jolla, California.
  • Vite CH; 2 Department of Neurology, Sidney Kimmel College of Medicine, Thomas Jefferson University , Philadelphia, Pennsylvania.
Hum Gene Ther ; 29(7): 785-801, 2018 07.
Article en En | MEDLINE | ID: mdl-29316812

Texto completo: 1 Colección: 01-internacional Banco de datos: MEDLINE Asunto principal: Terapia Genética / Enfermedades del Sistema Nervioso Periférico / Galactosilceramidasa / Leucodistrofia de Células Globoides Límite: Animals / Humans / Infant Idioma: En Revista: Hum Gene Ther Asunto de la revista: GENETICA MEDICA / TERAPEUTICA Año: 2018 Tipo del documento: Article

Texto completo: 1 Colección: 01-internacional Banco de datos: MEDLINE Asunto principal: Terapia Genética / Enfermedades del Sistema Nervioso Periférico / Galactosilceramidasa / Leucodistrofia de Células Globoides Límite: Animals / Humans / Infant Idioma: En Revista: Hum Gene Ther Asunto de la revista: GENETICA MEDICA / TERAPEUTICA Año: 2018 Tipo del documento: Article