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Pharmacokinetic modelling and validation of the half-life extension needed to reduce the burden of infusions compared with standard factor VIII.
Hermans, C; Mahlangu, J; Booth, J; Schütz, H; Santagostino, E; Young, G; Lee, H-Y; Steinitz-Trost, K N; Blanchette, V; Berntorp, E.
Afiliación
  • Hermans C; Haemostasis and Thrombosis Unit, Division of Haematology, Cliniques Universitaires Saint-Luc, Brussels, Belgium.
  • Mahlangu J; Faculty of Health Sciences, Charlotte Maxeke Johannesburg Academic Hospital, University of the Witwatersrand and National Health Laboratory Service, Johannesburg, South Africa.
  • Booth J; Shire, Cambridge, MA, USA.
  • Schütz H; BEBAC, Vienna, Austria.
  • Santagostino E; A. Bianchi Bonomi Hemophilia and Thrombosis Center, IRCCS Ca' Granda Foundation, Maggiore Hospital Policlinico of Milan, Milan, Italy.
  • Young G; Children's Hospital Los Angeles, University of Southern California Keck School of Medicine, Los Angeles, CA, USA.
  • Lee HY; Shire, Zurich, Switzerland.
  • Steinitz-Trost KN; Shire, Vienna, Austria.
  • Blanchette V; Department of Pediatrics, Division of Hematology/Oncology, The Hospital for Sick Children, University of Toronto, Toronto, Canada.
  • Berntorp E; Centre for Thrombosis and Haemostasis, Lund University, Malmö, Sweden.
Haemophilia ; 24(3): 376-384, 2018 May.
Article en En | MEDLINE | ID: mdl-29732708

Texto completo: 1 Colección: 01-internacional Banco de datos: MEDLINE Asunto principal: Proteínas Recombinantes / Factor VIII / Modelos Biológicos Tipo de estudio: Prognostic_studies Límite: Humans Idioma: En Revista: Haemophilia Asunto de la revista: HEMATOLOGIA Año: 2018 Tipo del documento: Article País de afiliación: Bélgica

Texto completo: 1 Colección: 01-internacional Banco de datos: MEDLINE Asunto principal: Proteínas Recombinantes / Factor VIII / Modelos Biológicos Tipo de estudio: Prognostic_studies Límite: Humans Idioma: En Revista: Haemophilia Asunto de la revista: HEMATOLOGIA Año: 2018 Tipo del documento: Article País de afiliación: Bélgica