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Special considerations for clinical trials in fibrodysplasia ossificans progressiva (FOP).
Hsiao, Edward C; Di Rocco, Maja; Cali, Amanda; Zasloff, Michael; Al Mukaddam, Mona; Pignolo, Robert J; Grunwald, Zvi; Netelenbos, Coen; Keen, Richard; Baujat, Genevieve; Brown, Matthew A; Cho, Tae-Joon; De Cunto, Carmen; Delai, Patricia; Haga, Nobuhiko; Morhart, Rolf; Scott, Christiaan; Zhang, Keqin; Diecidue, Robert J; Friedman, Clive S; Kaplan, Fredrick S; Eekhoff, Elisabeth M W.
Afiliación
  • Hsiao EC; Division of Endocrinology and Metabolism, and the Institute for Human Genetics, Department of Medicine, University of California, San Francisco, CA, USA.
  • Di Rocco M; Unit of Rare Diseases, Department of Pediatrics, IRCCS Giannina Gaslini Institute, Genoa, Italy.
  • Cali A; Radiant Hope Foundation and the Ian Cali FOP Research Fund, PENN Medicine, Center for Research in FOP & Related Disorders.
  • Zasloff M; Departments of Orthopaedic Surgery and Genetics, The Center for Research in FOP & Related Disorders, University of Pennsylvania School of Medicine; and MedStar Georgetown Transplant Institute Georgetown University School of Medicine, Washington, DC, USA.
  • Al Mukaddam M; Division of Endocrinology, Diabetes and Metabolism, Departments of Medicine and Orthopaedic Surgery, University of Pennsylvania School of Medicine, Philadelphia, PA, USA.
  • Pignolo RJ; Department of Medicine, Mayo Clinic, Rochester, MN, USA.
  • Grunwald Z; Department of Anesthesiology, Thomas Jefferson University, Philadelphia, PA, USA.
  • Netelenbos C; Department of Internal Medicine section Endocrinology, Amsterdam Bone Center, Amsterdam University Medical Centers location VUmc, Amsterdam, the Netherlands.
  • Keen R; Royal National Orthopaedic Hospital, Stanmore, UK.
  • Baujat G; Centre de Référence Maladies Osseuses Constitutionnelles, Departement de Génétique, Hôpital Necker-Enfants Malades, Institut Imagine, Paris, France.
  • Brown MA; Institute of Health and Biomedical Innovation, Queensland University of Technology, Translational Research Institute, Woolloongabba, QLD, Australia.
  • Cho TJ; Division of Pediatric Orthopaedics, Seoul National University Children's Hospital, Seoul, South Korea.
  • De Cunto C; Pediatric Rheumatology Section, Department of Pediatrics, Hospital Italiano de Buenos Aires, Ciudad Autónoma de Buenos Aires, Argentina.
  • Delai P; Hospital Israelita Albert Einstein, Instituto de Ensino e Pesquisa, São Paulo-SP, Brazil.
  • Haga N; Department of Rehabilitation Medicine, Graduate School of Medicine, University of Tokyo, Tokyo, Japan.
  • Morhart R; Department of Pediatrics, Klinikum Garmisch-Partenkirchen GmbH, Garmisch-Partenkirchen, Germany.
  • Scott C; Paediatric Rheumatology, Red Cross Children's Hospital, University of Cape Town, Cape Town, South Africa.
  • Zhang K; Department of Endocrinology, Tongji Hospital, Shanghai Tongji University, Shanghai, China.
  • Diecidue RJ; Sidney Kimmel Medical College, Thomas Jefferson University, Philadelphia, PA, USA.
  • Friedman CS; Schulich School of Medicine and Dentistry, Pediatric Oral Health and Dentistry, London, ON, Canada.
  • Kaplan FS; Departments of Medicine & Orthopaedic Surgery, Center for Research in FOP & Related Disorders, The Perelman School of Medicine, University of Pennsylvania, Philadelphia, PA, USA.
  • Eekhoff EMW; Department of Internal Medicine section Endocrinology, Amsterdam Bone Center, Amsterdam University Medical Centers location VUmc, Amsterdam, the Netherlands.
Br J Clin Pharmacol ; 85(6): 1199-1207, 2019 06.
Article en En | MEDLINE | ID: mdl-30281842

Texto completo: 1 Colección: 01-internacional Banco de datos: MEDLINE Asunto principal: Proyectos de Investigación / Ensayos Clínicos como Asunto / Remodelación Ósea / Osificación Heterotópica / Miositis Osificante Tipo de estudio: Diagnostic_studies / Guideline Límite: Humans Idioma: En Revista: Br J Clin Pharmacol Año: 2019 Tipo del documento: Article País de afiliación: Estados Unidos

Texto completo: 1 Colección: 01-internacional Banco de datos: MEDLINE Asunto principal: Proyectos de Investigación / Ensayos Clínicos como Asunto / Remodelación Ósea / Osificación Heterotópica / Miositis Osificante Tipo de estudio: Diagnostic_studies / Guideline Límite: Humans Idioma: En Revista: Br J Clin Pharmacol Año: 2019 Tipo del documento: Article País de afiliación: Estados Unidos