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Function and Immunogenicity of Gene-corrected iPSC-derived Hepatocyte-Like Cells in Restoring Low Density Lipoprotein Uptake in Homozygous Familial Hypercholesterolemia.
Okada, Hirofumi; Nakanishi, Chiaki; Yoshida, Shohei; Shimojima, Masaya; Yokawa, Junichiro; Mori, Masayuki; Tada, Hayato; Yoshimuta, Tsuyoshi; Hayashi, Kenshi; Yamano, Tomoyoshi; Hanayama, Rikinari; Yamagishi, Masakazu; Kawashiri, Masa-Aki.
Afiliación
  • Okada H; Department of Cardiovascular and Internal Medicine, Kanazawa University Graduate School of Medicine, Takara-machi 13-1, Kanazawa, Ishikawa, 920-8641, Japan.
  • Nakanishi C; Department of Cardiovascular and Internal Medicine, Kanazawa University Graduate School of Medicine, Takara-machi 13-1, Kanazawa, Ishikawa, 920-8641, Japan.
  • Yoshida S; Department of Cardiovascular and Internal Medicine, Kanazawa University Graduate School of Medicine, Takara-machi 13-1, Kanazawa, Ishikawa, 920-8641, Japan.
  • Shimojima M; Department of Cardiovascular and Internal Medicine, Kanazawa University Graduate School of Medicine, Takara-machi 13-1, Kanazawa, Ishikawa, 920-8641, Japan.
  • Yokawa J; Department of Cardiovascular and Internal Medicine, Kanazawa University Graduate School of Medicine, Takara-machi 13-1, Kanazawa, Ishikawa, 920-8641, Japan.
  • Mori M; Department of Cardiovascular and Internal Medicine, Kanazawa University Graduate School of Medicine, Takara-machi 13-1, Kanazawa, Ishikawa, 920-8641, Japan.
  • Tada H; Department of Cardiovascular and Internal Medicine, Kanazawa University Graduate School of Medicine, Takara-machi 13-1, Kanazawa, Ishikawa, 920-8641, Japan.
  • Yoshimuta T; Department of Cardiovascular and Internal Medicine, Kanazawa University Graduate School of Medicine, Takara-machi 13-1, Kanazawa, Ishikawa, 920-8641, Japan.
  • Hayashi K; Department of Cardiovascular and Internal Medicine, Kanazawa University Graduate School of Medicine, Takara-machi 13-1, Kanazawa, Ishikawa, 920-8641, Japan.
  • Yamano T; Department of Immunology, Kanazawa University Graduate School of Medicine, Takara-machi 13-1, Kanazawa, Ishikawa, 920-8640, Japan.
  • Hanayama R; Department of Immunology, Kanazawa University Graduate School of Medicine, Takara-machi 13-1, Kanazawa, Ishikawa, 920-8640, Japan.
  • Yamagishi M; Department of Cardiovascular and Internal Medicine, Kanazawa University Graduate School of Medicine, Takara-machi 13-1, Kanazawa, Ishikawa, 920-8641, Japan. m-yamagishi@kun.ohs.ac.jp.
  • Kawashiri MA; Department of Human Sciences, Osaka University of Human Sciences, 1-12-13 Shoya, Settsu, Osaka, 566-8501, Japan. m-yamagishi@kun.ohs.ac.jp.
Sci Rep ; 9(1): 4695, 2019 03 18.
Article en En | MEDLINE | ID: mdl-30886174

Texto completo: 1 Colección: 01-internacional Banco de datos: MEDLINE Asunto principal: Terapia Biológica / Terapia Genética / Hepatocitos / Células Madre Pluripotentes Inducidas / Hiperlipoproteinemia Tipo II / Lipoproteínas LDL Límite: Humans Idioma: En Revista: Sci Rep Año: 2019 Tipo del documento: Article País de afiliación: Japón

Texto completo: 1 Colección: 01-internacional Banco de datos: MEDLINE Asunto principal: Terapia Biológica / Terapia Genética / Hepatocitos / Células Madre Pluripotentes Inducidas / Hiperlipoproteinemia Tipo II / Lipoproteínas LDL Límite: Humans Idioma: En Revista: Sci Rep Año: 2019 Tipo del documento: Article País de afiliación: Japón