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CRISPR/Cas9-mediated gene correction in hemophilia B patient-derived iPSCs.
Morishige, Satoshi; Mizuno, Shinichi; Ozawa, Hidetoshi; Nakamura, Takayuki; Mazahery, Ahmad; Nomura, Kei; Seki, Ritsuko; Mouri, Fumihiko; Osaki, Koichi; Yamamura, Kenichi; Okamura, Takashi; Nagafuji, Koji.
Afiliación
  • Morishige S; Division of Hematology and Oncology, Department of Medicine, Kurume University School of Medicine, 67 Asahi-machi, Kurume, 830-0011, Japan.
  • Mizuno S; Division of Hematology and Oncology, Department of Medicine, Kurume University School of Medicine, 67 Asahi-machi, Kurume, 830-0011, Japan.
  • Ozawa H; Center for Advanced Medical Innovation, Kyushu University, 3-1-1 Maidashi, Higashi-Ku, Fukuoka, 812-8582, Japan.
  • Nakamura T; Division of Hematology and Oncology, Department of Medicine, Kurume University School of Medicine, 67 Asahi-machi, Kurume, 830-0011, Japan.
  • Mazahery A; Division of Hematology and Oncology, Department of Medicine, Kurume University School of Medicine, 67 Asahi-machi, Kurume, 830-0011, Japan.
  • Nomura K; Institute of Resource Development and Analysis, Kumamoto University, 2-2-1 Honjo, Chuo-ku, Kumamoto, 860-0811, Japan.
  • Seki R; Division of Hematology and Oncology, Department of Medicine, Kurume University School of Medicine, 67 Asahi-machi, Kurume, 830-0011, Japan.
  • Mouri F; Division of Hematology and Oncology, Department of Medicine, Kurume University School of Medicine, 67 Asahi-machi, Kurume, 830-0011, Japan.
  • Osaki K; Division of Hematology and Oncology, Department of Medicine, Kurume University School of Medicine, 67 Asahi-machi, Kurume, 830-0011, Japan.
  • Yamamura K; Division of Hematology and Oncology, Department of Medicine, Kurume University School of Medicine, 67 Asahi-machi, Kurume, 830-0011, Japan.
  • Okamura T; Institute of Resource Development and Analysis, Kumamoto University, 2-2-1 Honjo, Chuo-ku, Kumamoto, 860-0811, Japan.
  • Nagafuji K; Division of Hematology and Oncology, Department of Medicine, Kurume University School of Medicine, 67 Asahi-machi, Kurume, 830-0011, Japan.
Int J Hematol ; 111(2): 225-233, 2020 Feb.
Article en En | MEDLINE | ID: mdl-31664646

Texto completo: 1 Colección: 01-internacional Banco de datos: MEDLINE Asunto principal: Terapia Genética / Hemofilia B / Células Madre Pluripotentes Inducidas / Sistemas CRISPR-Cas / Edición Génica Límite: Humans Idioma: En Revista: Int J Hematol Asunto de la revista: HEMATOLOGIA Año: 2020 Tipo del documento: Article País de afiliación: Japón

Texto completo: 1 Colección: 01-internacional Banco de datos: MEDLINE Asunto principal: Terapia Genética / Hemofilia B / Células Madre Pluripotentes Inducidas / Sistemas CRISPR-Cas / Edición Génica Límite: Humans Idioma: En Revista: Int J Hematol Asunto de la revista: HEMATOLOGIA Año: 2020 Tipo del documento: Article País de afiliación: Japón