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Towards a global multidisciplinary consensus framework on haemophilia gene therapy: Report of the 2nd World Federation of Haemophilia Gene Therapy Round Table.
Pierce, Glenn F; Pasi, K John; Coffin, Donna; Kaczmarek, Radoslaw; Lillicrap, David; Mahlangu, Johnny; Rottellini, Dawn; Sannié, Thomas; Srivastava, Alok; VandenDriessche, Thierry; Weill, Alain.
Afiliación
  • Pierce GF; World Federation of Hemophilia, Montreal, QC, Canada.
  • Pasi KJ; Royal London Haemophilia Centre, Barts and The London School of Medicine and Dentistry, London, UK.
  • Coffin D; World Federation of Hemophilia, Montreal, QC, Canada.
  • Kaczmarek R; Department of Pediatrics, Indiana University School of Medicine, Indianapolis, IN, USA.
  • Lillicrap D; Laboratory of Glycobiology, Hirszfeld Institute of Immunology and Experimental Therapy, Wroclaw, Poland.
  • Mahlangu J; Department of Pathology & Molecular Medicine, Queen's University, Kingston, ON, Canada.
  • Rottellini D; Haemophilia Comprehensive Care Centre, NHLS and Charlotte Maxeke Johannesburg Academic Hospital, University of the Witwatersrand, Johannesburg, South Africa.
  • Sannié T; National Hemophilia Foundation, New York, NY, USA.
  • Srivastava A; French Haemophilia Association (AFH), Paris, France.
  • VandenDriessche T; Department of Haematology, Christian Medical College Vellore, Vellore, India.
  • Weill A; Department of Gene Therapy & Regenerative Medicine, Vrije Universiteit Brussel (VUB), Brussels, Belgium.
Haemophilia ; 26(3): 443-449, 2020 May.
Article en En | MEDLINE | ID: mdl-32202382

Texto completo: 1 Colección: 01-internacional Banco de datos: MEDLINE Asunto principal: Terapia Genética / Hemofilia A Tipo de estudio: Guideline / Health_technology_assessment / Prognostic_studies / Qualitative_research Límite: Humans Idioma: En Revista: Haemophilia Asunto de la revista: HEMATOLOGIA Año: 2020 Tipo del documento: Article País de afiliación: Canadá

Texto completo: 1 Colección: 01-internacional Banco de datos: MEDLINE Asunto principal: Terapia Genética / Hemofilia A Tipo de estudio: Guideline / Health_technology_assessment / Prognostic_studies / Qualitative_research Límite: Humans Idioma: En Revista: Haemophilia Asunto de la revista: HEMATOLOGIA Año: 2020 Tipo del documento: Article País de afiliación: Canadá