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A tailored Cln3Q352X mouse model for testing therapeutic interventions in CLN3 Batten disease.
Langin, Logan; Johnson, Tyler B; Kovács, Attila D; Pearce, David A; Weimer, Jill M.
Afiliación
  • Langin L; Pediatrics and Rare Diseases Group, Sanford Research, 2301 E. 60th N, Sioux Falls, SD, 57104, USA.
  • Johnson TB; Pediatrics and Rare Diseases Group, Sanford Research, 2301 E. 60th N, Sioux Falls, SD, 57104, USA.
  • Kovács AD; Pediatrics and Rare Diseases Group, Sanford Research, 2301 E. 60th N, Sioux Falls, SD, 57104, USA.
  • Pearce DA; Department of Pediatrics, Sanford School of Medicine, University of South Dakota, Sioux Falls, SD, USA.
  • Weimer JM; Pediatrics and Rare Diseases Group, Sanford Research, 2301 E. 60th N, Sioux Falls, SD, 57104, USA. david.pearce@sanfordhealth.org.
Sci Rep ; 10(1): 10591, 2020 06 29.
Article en En | MEDLINE | ID: mdl-32601357

Texto completo: 1 Colección: 01-internacional Banco de datos: MEDLINE Asunto principal: Glicoproteínas de Membrana / Chaperonas Moleculares Límite: Animals Idioma: En Revista: Sci Rep Año: 2020 Tipo del documento: Article País de afiliación: Estados Unidos

Texto completo: 1 Colección: 01-internacional Banco de datos: MEDLINE Asunto principal: Glicoproteínas de Membrana / Chaperonas Moleculares Límite: Animals Idioma: En Revista: Sci Rep Año: 2020 Tipo del documento: Article País de afiliación: Estados Unidos