Your browser doesn't support javascript.
loading
Long-term efficacy of olipudase alfa in adults with acid sphingomyelinase deficiency (ASMD): Further clearance of hepatic sphingomyelin is associated with additional improvements in pro- and anti-atherogenic lipid profiles after 42 months of treatment.
Thurberg, Beth L; Diaz, George A; Lachmann, Robin H; Schiano, Thomas; Wasserstein, Melissa P; Ji, Allena J; Zaher, Atef; Peterschmitt, M Judith.
Afiliación
  • Thurberg BL; Department of Pathology, Sanofi Genzyme, Cambridge, MA, United States of America. Electronic address: Beth.Thurberg@sanofi.com.
  • Diaz GA; Genetics and Genomics Sciences, Icahn School of Medicine at Mount Sinai, New York, NY, United States of America.
  • Lachmann RH; National Hospital for Neurology and Neurosurgery, London, UK.
  • Schiano T; Genetics and Genomics Sciences, Icahn School of Medicine at Mount Sinai, New York, NY, United States of America.
  • Wasserstein MP; Children's Hospital at Montefiore, Albert Einstein College of Medicine, Bronx, NY, United States of America.
  • Ji AJ; Biomarkers and Clinical Bioanalysis, Sanofi Genzyme, Framingham, MA, United States of America.
  • Zaher A; Clinical Development, Sanofi Genzyme, Cambridge, MA, United States of America.
  • Peterschmitt MJ; Clinical Development, Sanofi Genzyme, Cambridge, MA, United States of America.
Mol Genet Metab ; 131(1-2): 245-252, 2020.
Article en En | MEDLINE | ID: mdl-32620536
Asunto(s)
Palabras clave
Texto completo
Imprimir
XML
PubMed Links
Buscar en Google

Texto completo: 1 Colección: 01-internacional Banco de datos: MEDLINE Asunto principal: Esfingomielina Fosfodiesterasa / Proteínas Recombinantes / Aterosclerosis Tipo de estudio: Clinical_trials / Risk_factors_studies Límite: Adolescent / Adult / Aged / Female / Humans / Male / Middle aged Idioma: En Revista: Mol Genet Metab Asunto de la revista: BIOLOGIA MOLECULAR / BIOQUIMICA / METABOLISMO Año: 2020 Tipo del documento: Article
Texto completo
Imprimir
XML
PubMed Links
Buscar en Google

Texto completo: 1 Colección: 01-internacional Banco de datos: MEDLINE Asunto principal: Esfingomielina Fosfodiesterasa / Proteínas Recombinantes / Aterosclerosis Tipo de estudio: Clinical_trials / Risk_factors_studies Límite: Adolescent / Adult / Aged / Female / Humans / Male / Middle aged Idioma: En Revista: Mol Genet Metab Asunto de la revista: BIOLOGIA MOLECULAR / BIOQUIMICA / METABOLISMO Año: 2020 Tipo del documento: Article