Access to medicines for rare diseases: beating the drum for primary ciliary dyskinesia.
ERJ Open Res
; 6(3)2020 Jul.
Article
en En
| MEDLINE
| ID: mdl-32964005
ABSTRACT
Primary ciliary dyskinesia, a rare disease causing bronchiectasis, lacks a sound evidence base for treatment. @beatpcd proposes 1) forming a PCD European clinical trial network to address this situation and 2) conducting n-of-1 trials to access medication. https//bit.ly/3j5blfM.
Texto completo:
1
Colección:
01-internacional
Banco de datos:
MEDLINE
Idioma:
En
Revista:
ERJ Open Res
Año:
2020
Tipo del documento:
Article
País de afiliación:
Noruega