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Clinical trials in pediatric ALS: a TRICALS feasibility study.
Kliest, Tessa; Van Eijk, Ruben P A; Al-Chalabi, Ammar; Albanese, Alberto; Andersen, Peter M; Amador, Maria Del Mar; BrÅthen, Geir; Brunaud-Danel, Veronique; Brylev, Lev; Camu, William; De Carvalho, Mamede; Cereda, Cristina; Cetin, Hakan; Chaverri, Delia; Chiò, Adriano; Corcia, Philippe; Couratier, Philippe; De Marchi, Fabiola; Desnuelle, Claude; Van Es, Michael A; Esteban, JesÚs; Filosto, Massimiliano; GarcÍa Redondo, Alberto; Grosskreutz, Julian; Hanemann, Clemens O; HolmØy, Trygve; HØyer, Helle; Ingre, Caroline; Koritnik, Blaz; Kuzma-Kozakiewicz, Magdalena; Lambert, Thomas; Leigh, Peter N; Lunetta, Christian; Mandrioli, Jessica; Mcdermott, Christopher J; Meyer, Thomas; Mora, Jesus S; Petri, Susanne; Povedano, MÓnica; Reviers, Evy; Riva, Nilo; Roes, Kit C B; Rubio, Miguel Á; Salachas, FranÇois; Sarafov, Stayko; SorarÙ, Gianni; Stevic, Zorica; Svenstrup, Kirsten; MØller, Anette Torvin; Turner, Martin R.
Afiliación
  • Kliest T; Department of Neurology, UMC Utrecht Brain Centre, University Medical Centre Utrecht, Utrecht, the Netherlands.
  • Van Eijk RPA; Department of Neurology, UMC Utrecht Brain Centre, University Medical Centre Utrecht, Utrecht, the Netherlands.
  • Al-Chalabi A; Biostatistics & Research Support, Julius Centre for Health Sciences and Primary Care, University Medical Centre Utrecht, Utrecht, the Netherlands.
  • Albanese A; Department of Basic and Clinical Neuroscience, King's College London, Maurice Wohl Clinical Neuroscience Institute, London, UK.
  • Andersen PM; Department of Neurology, King's College Hospital, London, UK.
  • Amador MDM; IRCCS Humanitas Research Hospital Rozzano, Milan, Italy.
  • BrÅthen G; Department of Clinical Sciences, Neurosciences, Umeå University, Umeå, Sweden.
  • Brunaud-Danel V; Département de Neurologie, Centre de référence SLA Ile de France.
  • Brylev L; Hôpital de la Pitié Salpêtrière, AP-HP, Paris, France.
  • Camu W; Department of Neurology, University Hospital of Trondheim, Trondheim, Norway.
  • De Carvalho M; Department of Neuromedicine and Movement Science, Norwegian University of Science and Technology, Trondheim, Norway.
  • Cereda C; ALS centre, CHU, University of Lille Nord de France, Lille, France.
  • Cetin H; Bujanov Moscow City Clinical Hospital, Moscow, Russian Federation.
  • Chaverri D; Moscow Research and Clinical Center for Neuropsychiatry of the Healthcare Department, Moscow, Russian Federation.
  • Chiò A; ALS Centre CHU Gui de Chauliac, University of Montpellier, Montpellier, France.
  • Corcia P; Institute of Physiology-Instituto de Medicina Molecular, Faculty of Medicine, University of Lisbon, Lisbon, Portugal.
  • Couratier P; Department of Neurosciences and Mental Health, H Santa Maria-CHLN, Lisbon, Portugal.
  • De Marchi F; Regional Newborn Screening Laboratory, Vittore Buzzi Children's Hospital-University of Milan, Italy.
  • Desnuelle C; Department of Neurology, Medical University of Vienna, Vienna, Austria.
  • Van Es MA; Neurology Service, Hospital Universitario La Paz, Madrid, Spain.
  • Esteban J; 'Rita Levi Montalcini' Department of Neuroscience, ALS Centre, University of Torino, Turin, Italy.
  • Filosto M; Azienda Ospedaliera Città della Salute e della Scienza, Turin, Italy.
  • GarcÍa Redondo A; Centre Constitutif SLA, CHRU de Tours - Fédération des centres SLA Tours-Limoges, LitORALS, Tours, France.
  • Grosskreutz J; Centre Constitutif de reference SLA-Fédération Tours-Limoges, CHU de Limoges, Limoges, France.
  • Hanemann CO; "Maggiore della Carità" University Hospital, Novara, Italy.
  • HolmØy T; Hôpital Pasteur 2 - CHU de Nice, Nice, France.
  • HØyer H; Department of Neurology, UMC Utrecht Brain Centre, University Medical Centre Utrecht, Utrecht, the Netherlands.
  • Ingre C; ALS Research Lab - ALS Unit, Instituto de Investigación Sanitaria Hospital 12 de Octubre "i + 12", CIBERER, Madrid, Spain.
  • Koritnik B; Department of Clinical and Experimental Sciences, University of Brescia; NeMO-Brescia Clinical Center for Neuromuscular Diseases, Brescia, Italy.
  • Kuzma-Kozakiewicz M; ALS Research Lab - ALS Unit, Instituto de Investigación Sanitaria Hospital 12 de Octubre "i + 12", CIBERER, Madrid, Spain.
  • Lambert T; Precision Neurology, Dept. of Neurology, Lübeck University Hospital, Lübeck, Germany.
  • Leigh PN; University of Plymouth, Peninsula Schools of Medicine and Dentistry, Plymouth, UK.
  • Lunetta C; Department of Neurology, Akershus University Hospital, Lørenskog, Norway.
  • Mandrioli J; Institute of Clinical Medicine, University of Oslo, Oslo, Norway.
  • Mcdermott CJ; Department of Medical Genetics, Telemark Hospital, Skien, Norway.
  • Meyer T; Department of Neurology, Karolinska University Hospital, Stockholm, Sweden.
  • Mora JS; Department of Clinical Neuroscience, Karolinska Institutet, Stockholm, Sweden.
  • Petri S; Institute of Clinical Neurophysiology, University Medical Centre Ljubljana, Ljubljana, Slovenia.
  • Povedano M; Department of Neurology, Medical University of Warsaw, Warsaw, Poland.
  • Reviers E; Department of Neurology, Royal Stoke University Hospital, Stoke, United Kingdom.
  • Riva N; Department of Neuroscience, Brighton and Sussex Medical School, Trafford Centre for Biomedical Research, University of Sussex, Brighton, UK.
  • Roes KCB; NEMO Clinical Center, Serena Onlus Foundation, Milan, Italy.
  • Rubio MÁ; NEMO LAB, Milan, Italy.
  • Salachas F; Department of Biomedical, Metabolic and Neural Sciences, Center for Neuroscience and Neurotechnology, University of Modena and Reggio Emilia, Modena, Italy.
  • Sarafov S; Department of Neuroscience, St. Agostino Estense Hospital, Azienda Ospedaliero Universitaria di Modena, Modena, Italy.
  • SorarÙ G; Department of Neuroscience, University of Sheffield, Sheffield Institute for Translational Neuroscience, Sheffield, United Kingdom.
  • Stevic Z; ALS Outpatient Department, Charité - Universitatsmedizin Berlin, Berlin, Germany.
  • Svenstrup K; ALS Unit/Neurology, Hospital San Rafael, Madrid, Spain.
  • MØller AT; Department of Neurology, Hannover Medical School, Hannover, Germany.
  • Turner MR; Functional Unit of Amyotrophic Lateral Sclerosis (UFELA), Service of Neurology, Bellvitge University Hospital, Hospitalet de Llobregat, Spain.
Article en En | MEDLINE | ID: mdl-35172656

Texto completo: 1 Colección: 01-internacional Banco de datos: MEDLINE Asunto principal: Esclerosis Amiotrófica Lateral Tipo de estudio: Diagnostic_studies / Prevalence_studies / Prognostic_studies / Risk_factors_studies Límite: Adult / Child / Humans País/Región como asunto: Europa Idioma: En Revista: Amyotroph Lateral Scler Frontotemporal Degener Año: 2022 Tipo del documento: Article País de afiliación: Países Bajos

Texto completo: 1 Colección: 01-internacional Banco de datos: MEDLINE Asunto principal: Esclerosis Amiotrófica Lateral Tipo de estudio: Diagnostic_studies / Prevalence_studies / Prognostic_studies / Risk_factors_studies Límite: Adult / Child / Humans País/Región como asunto: Europa Idioma: En Revista: Amyotroph Lateral Scler Frontotemporal Degener Año: 2022 Tipo del documento: Article País de afiliación: Países Bajos