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Selumetinib in children with neurofibromatosis type 1 and asymptomatic inoperable plexiform neurofibroma at risk for developing tumor-related morbidity.
Gross, Andrea M; Glassberg, Brittany; Wolters, Pamela L; Dombi, Eva; Baldwin, Andrea; Fisher, Michael J; Kim, AeRang; Bornhorst, Miriam; Weiss, Brian D; Blakeley, Jaishri O; Whitcomb, Patricia; Paul, Scott M; Steinberg, Seth M; Venzon, David J; Martin, Staci; Carbonell, Amanda; Heisey, Kara; Therrien, Janet; Kapustina, Oxana; Dufek, Anne; Derdak, Joanne; Smith, Malcolm A; Widemann, Brigitte C.
Afiliación
  • Gross AM; Pediatric Oncology Branch, Center for Cancer research, National Cancer Institute, Bethesda, Maryland, USA.
  • Glassberg B; Pediatric Oncology Branch, Center for Cancer research, National Cancer Institute, Bethesda, Maryland, USA.
  • Wolters PL; Pediatric Oncology Branch, Center for Cancer research, National Cancer Institute, Bethesda, Maryland, USA.
  • Dombi E; Pediatric Oncology Branch, Center for Cancer research, National Cancer Institute, Bethesda, Maryland, USA.
  • Baldwin A; Pediatric Oncology Branch, Center for Cancer research, National Cancer Institute, Bethesda, Maryland, USA.
  • Fisher MJ; Division of Oncology, Children's Hospital of Philadelphia, Philadelphia, Pennsylvania, USA.
  • Kim A; Center for Cancer and Blood Disorders, Children's National Hospital, Washington, DC, USA.
  • Bornhorst M; Center for Cancer and Blood Disorders, Children's National Hospital, Washington, DC, USA.
  • Weiss BD; Cincinnati Children's Hospital Medical Center, Cincinnati, Ohio, USA.
  • Blakeley JO; Department of Neurology, Johns Hopkins University, Baltimore, Maryland, USA.
  • Whitcomb P; Pediatric Oncology Branch, Center for Cancer research, National Cancer Institute, Bethesda, Maryland, USA.
  • Paul SM; Rehabilitation Medicine Department, NIH Clinical Center, Baltimore, Maryland, USA.
  • Steinberg SM; Biostatistics and Data Management Section, Center for Cancer Research, National Cancer Institute, Baltimore, Maryland, USA.
  • Venzon DJ; Biostatistics and Data Management Section, Center for Cancer Research, National Cancer Institute, Baltimore, Maryland, USA.
  • Martin S; Pediatric Oncology Branch, Center for Cancer research, National Cancer Institute, Bethesda, Maryland, USA.
  • Carbonell A; Pediatric Oncology Branch, Center for Cancer research, National Cancer Institute, Bethesda, Maryland, USA.
  • Heisey K; Pediatric Oncology Branch, Center for Cancer research, National Cancer Institute, Bethesda, Maryland, USA.
  • Therrien J; Pediatric Oncology Branch, Center for Cancer research, National Cancer Institute, Bethesda, Maryland, USA.
  • Kapustina O; Pediatric Oncology Branch, Center for Cancer research, National Cancer Institute, Bethesda, Maryland, USA.
  • Dufek A; Pediatric Oncology Branch, Center for Cancer research, National Cancer Institute, Bethesda, Maryland, USA.
  • Derdak J; Pediatric Oncology Branch, Center for Cancer research, National Cancer Institute, Bethesda, Maryland, USA.
  • Smith MA; Cancer Therapy Evaluation Program, National Cancer Institute, Bethesda, Maryland, USA (M.A.S.).
  • Widemann BC; Pediatric Oncology Branch, Center for Cancer research, National Cancer Institute, Bethesda, Maryland, USA.
Neuro Oncol ; 24(11): 1978-1988, 2022 11 02.
Article en En | MEDLINE | ID: mdl-35467749

Texto completo: 1 Colección: 01-internacional Banco de datos: MEDLINE Asunto principal: Neurofibromatosis 1 / Neurofibroma Plexiforme Tipo de estudio: Etiology_studies / Observational_studies / Risk_factors_studies Límite: Child / Humans Idioma: En Revista: Neuro Oncol Asunto de la revista: NEOPLASIAS / NEUROLOGIA Año: 2022 Tipo del documento: Article País de afiliación: Estados Unidos

Texto completo: 1 Colección: 01-internacional Banco de datos: MEDLINE Asunto principal: Neurofibromatosis 1 / Neurofibroma Plexiforme Tipo de estudio: Etiology_studies / Observational_studies / Risk_factors_studies Límite: Child / Humans Idioma: En Revista: Neuro Oncol Asunto de la revista: NEOPLASIAS / NEUROLOGIA Año: 2022 Tipo del documento: Article País de afiliación: Estados Unidos