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Long-Term Safety and Efficacy of Elexacaftor/Tezacaftor/Ivacaftor in Children Aged ⩾6 Years with Cystic Fibrosis and at Least One F508del Allele: A Phase 3, Open-Label Clinical Trial.
Wainwright, Claire; McColley, Susanna A; McNally, Paul; Powers, Michael; Ratjen, Felix; Rayment, Jonathan H; Retsch-Bogart, George; Roesch, Erica; Ahluwalia, Neil; Chin, Anna; Chu, Chenghao; Lu, Mengdi; Menon, Prema; Waltz, David; Weinstock, Tanya; Zelazoski, Laura; Davies, Jane C.
Afiliación
  • Wainwright C; Queensland Children's Hospital, South Brisbane, Queensland, Australia.
  • McColley SA; Child Health Research Centre, University of Queensland, South Brisbane, Queensland, Australia.
  • McNally P; Ann & Robert H. Lurie Children's Hospital of Chicago, Chicago, Illinois.
  • Powers M; Northwestern University Feinberg School of Medicine, Chicago, Illinois.
  • Ratjen F; Children's Health Ireland, Dublin, Ireland.
  • Rayment JH; Royal College of Surgeons in Ireland University of Medicine and Health Sciences, Dublin, Ireland.
  • Retsch-Bogart G; Oregon Health & Sciences University, Portland, Oregon.
  • Roesch E; University of Toronto, Toronto, Ontario, Canada.
  • Ahluwalia N; University of British Columbia, Vancouver, British Columbia, Canada.
  • Chin A; University of North Carolina at Chapel Hill, Chapel Hill, North Carolina.
  • Chu C; University Hospitals Cleveland Medical Center, Cleveland, Ohio.
  • Lu M; Vertex Pharmaceuticals Incorporated, Boston, Massachusetts.
  • Menon P; Vertex Pharmaceuticals Incorporated, Boston, Massachusetts.
  • Waltz D; Vertex Pharmaceuticals Incorporated, Boston, Massachusetts.
  • Weinstock T; Vertex Pharmaceuticals Incorporated, Boston, Massachusetts.
  • Zelazoski L; Vertex Pharmaceuticals Incorporated, Boston, Massachusetts.
  • Davies JC; Vertex Pharmaceuticals Incorporated, Boston, Massachusetts.
Am J Respir Crit Care Med ; 208(1): 68-78, 2023 07 01.
Article en En | MEDLINE | ID: mdl-37154609

Texto completo: 1 Colección: 01-internacional Banco de datos: MEDLINE Asunto principal: Fibrosis Quística Tipo de estudio: Clinical_trials / Diagnostic_studies / Prognostic_studies Límite: Adult / Child / Humans Idioma: En Revista: Am J Respir Crit Care Med Asunto de la revista: TERAPIA INTENSIVA Año: 2023 Tipo del documento: Article País de afiliación: Australia

Texto completo: 1 Colección: 01-internacional Banco de datos: MEDLINE Asunto principal: Fibrosis Quística Tipo de estudio: Clinical_trials / Diagnostic_studies / Prognostic_studies Límite: Adult / Child / Humans Idioma: En Revista: Am J Respir Crit Care Med Asunto de la revista: TERAPIA INTENSIVA Año: 2023 Tipo del documento: Article País de afiliación: Australia