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Use of External Control Cohorts in Pediatric Brain Tumor Clinical Trials.
Margol, Ashley S; Molinaro, Annette M; Onar-Thomas, Arzu; Resnick, Adam; Hanson, Derek; Kieran, Mark; Mishra-Kalyani, Pallavi; Rivera, Donna; Barone, Amy; Arons, David; Meehan, Clair; Prados, Michael.
Afiliación
  • Margol AS; Keck School of Medicine of University of Southern California, Cancer and Blood Disease Institute at Children's Hospital Los Angeles, Los Angeles, CA.
  • Molinaro AM; Division of Biomedical Statistics and Informatics, Department of Neurosurgery, University of California, San Francisco, San Francisco, CA.
  • Onar-Thomas A; St Jude Children's Research Hospital, Memphis, TN.
  • Resnick A; Center for Data Driven Discovery in Biomedicine, Children's Hospital of Philadelphia, Philadelphia, PA.
  • Hanson D; Joseph M. Sanzari Children's Hospital at Hackensack University Medical Center, Hackensack, NJ.
  • Kieran M; Day One Biopharmaceuticals, Brisbane, CA.
  • Mishra-Kalyani P; US Food and Drug Administration, Washington, DC.
  • Rivera D; US Food and Drug Administration, Washington, DC.
  • Barone A; US Food and Drug Administration, Washington, DC.
  • Arons D; National Brain Tumor Society, Newton, MA.
  • Meehan C; National Brain Tumor Society, Newton, MA.
  • Prados M; Departments of Neurosurgery and Pediatrics, University of California, San Francisco, San Francisco, CA.
J Clin Oncol ; 42(12): 1340-1343, 2024 Apr 20.
Article en En | MEDLINE | ID: mdl-38394473
ABSTRACT
Why, when, and how to consider external control cohorts in pediatric brain tumor clinical trials.
Asunto(s)

Texto completo: 1 Colección: 01-internacional Banco de datos: MEDLINE Asunto principal: Neoplasias Encefálicas Límite: Child / Humans Idioma: En Revista: J Clin Oncol Año: 2024 Tipo del documento: Article

Texto completo: 1 Colección: 01-internacional Banco de datos: MEDLINE Asunto principal: Neoplasias Encefálicas Límite: Child / Humans Idioma: En Revista: J Clin Oncol Año: 2024 Tipo del documento: Article