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Advancing gene targeting for primary immune deficiencies: Adenine base editing of the human IL2RG locus for correction of SCID-X1.
McIvor, R Scott; Eaton, Ella J; Webber, Beau R; Moriarity, Branden S.
Afiliación
  • McIvor RS; Department of Genetics, Cell Biology and Development, University of Minnesota, Minneapolis, MN 55455, USA; Center for Genome Engineering, University of Minnesota, Minneapolis, MN 55455, USA; Masonic Cancer Center, University of Minnesota, Minneapolis, MN 55455, USA; Stem Cell Institute, University o
  • Eaton EJ; Department of Genetics, Cell Biology and Development, University of Minnesota, Minneapolis, MN 55455, USA; Center for Genome Engineering, University of Minnesota, Minneapolis, MN 55455, USA.
  • Webber BR; Center for Genome Engineering, University of Minnesota, Minneapolis, MN 55455, USA; Masonic Cancer Center, University of Minnesota, Minneapolis, MN 55455, USA; Stem Cell Institute, University of Minnesota, Minneapolis, MN 55455, USA; Department of Pediatrics, University of Minnesota, Minneapolis, MN
  • Moriarity BS; Center for Genome Engineering, University of Minnesota, Minneapolis, MN 55455, USA; Masonic Cancer Center, University of Minnesota, Minneapolis, MN 55455, USA; Stem Cell Institute, University of Minnesota, Minneapolis, MN 55455, USA; Department of Pediatrics, University of Minnesota, Minneapolis, MN
Mol Ther ; 32(6): 1606-1608, 2024 Jun 05.
Article en En | MEDLINE | ID: mdl-38781958

Texto completo: 1 Colección: 01-internacional Banco de datos: MEDLINE Asunto principal: Enfermedades por Inmunodeficiencia Combinada Ligada al Cromosoma X / Subunidad gamma Común de Receptores de Interleucina / Edición Génica Límite: Animals / Humans Idioma: En Revista: Mol Ther / Mol. ther / Molecular therapy Asunto de la revista: BIOLOGIA MOLECULAR / TERAPEUTICA Año: 2024 Tipo del documento: Article

Texto completo: 1 Colección: 01-internacional Banco de datos: MEDLINE Asunto principal: Enfermedades por Inmunodeficiencia Combinada Ligada al Cromosoma X / Subunidad gamma Común de Receptores de Interleucina / Edición Génica Límite: Animals / Humans Idioma: En Revista: Mol Ther / Mol. ther / Molecular therapy Asunto de la revista: BIOLOGIA MOLECULAR / TERAPEUTICA Año: 2024 Tipo del documento: Article