Expanded-access use of elamipretide in a patient with membrane protein-associated neurodegeneration.
Clin Case Rep
; 12(7): e9116, 2024 Jul.
Article
en En
| MEDLINE
| ID: mdl-38919884
ABSTRACT
This case report presents a progressively declining 17-year-old patient with membrane protein-associated neurodegeneration who demonstrated symptomatic improvements in her dysarthria, dysphagia, and gait, and objective improvements in her 6-minute walk test and 5 times sit-to-stand test during elamipretide treatment.
Texto completo:
1
Colección:
01-internacional
Banco de datos:
MEDLINE
Idioma:
En
Revista:
Clin Case Rep
Año:
2024
Tipo del documento:
Article