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A reduced-toxicity regimen is associated with durable engraftment and clinical cure of nonmalignant genetic diseases among children undergoing blood and marrow transplantation with an HLA-matched related donor.
Mahadeo, Kris Michael; Weinberg, Kenneth I; Abdel-Azim, Hisham; Miklos, David B; Killen, Renna; Kohn, Donald; Crooks, Gay M; Shah, Ami J; Kharbanda, Sandhya; Agarwal, Rajni; Kapoor, Neena.
Afiliação
  • Mahadeo KM; Pediatric Blood and Marrow Transplantation Program, Children's Hospital at Montefiore, Albert Einstein College of Medicine, Bronx, New York. Electronic address: kmahadeo@montefiore.org.
  • Weinberg KI; Pediatric Stem Cell Transplantation, Lucille Packard Children's Hospital, Stanford University, Palo Alto, California.
  • Abdel-Azim H; Division of Hematology, Oncology and Blood & Marrow Transplantation, Children's Hospital Los Angeles, University of Southern California, Los Angeles, California.
  • Miklos DB; Pediatric Stem Cell Transplantation, Lucille Packard Children's Hospital, Stanford University, Palo Alto, California.
  • Killen R; Division of Hematology, Oncology and Blood & Marrow Transplantation, Children's Hospital Los Angeles, University of Southern California, Los Angeles, California.
  • Kohn D; Division of Hematology, Oncology and Blood & Marrow Transplantation, Mattel Children's Hospital, University California Los Angeles, Los Angeles, California.
  • Crooks GM; Division of Hematology, Oncology and Blood & Marrow Transplantation, Mattel Children's Hospital, University California Los Angeles, Los Angeles, California.
  • Shah AJ; Division of Hematology, Oncology and Blood & Marrow Transplantation, Mattel Children's Hospital, University California Los Angeles, Los Angeles, California.
  • Kharbanda S; Pediatric Stem Cell Transplantation, Lucille Packard Children's Hospital, Stanford University, Palo Alto, California.
  • Agarwal R; Pediatric Stem Cell Transplantation, Lucille Packard Children's Hospital, Stanford University, Palo Alto, California.
  • Kapoor N; Division of Hematology, Oncology and Blood & Marrow Transplantation, Children's Hospital Los Angeles, University of Southern California, Los Angeles, California.
Biol Blood Marrow Transplant ; 21(3): 440-4, 2015 Mar.
Article em En | MEDLINE | ID: mdl-25459642

Texto completo: 1 Coleções: 01-internacional Base de dados: MEDLINE Assunto principal: Transplante de Medula Óssea / Condicionamento Pré-Transplante / Agonistas Mieloablativos / Sobrevivência de Enxerto / Doenças Genéticas Inatas Tipo de estudo: Clinical_trials / Observational_studies / Prognostic_studies / Risk_factors_studies Limite: Adolescent / Adult / Child / Child, preschool / Female / Humans / Infant / Male Idioma: En Revista: Biol Blood Marrow Transplant Assunto da revista: HEMATOLOGIA / TRANSPLANTE Ano de publicação: 2015 Tipo de documento: Article

Texto completo: 1 Coleções: 01-internacional Base de dados: MEDLINE Assunto principal: Transplante de Medula Óssea / Condicionamento Pré-Transplante / Agonistas Mieloablativos / Sobrevivência de Enxerto / Doenças Genéticas Inatas Tipo de estudo: Clinical_trials / Observational_studies / Prognostic_studies / Risk_factors_studies Limite: Adolescent / Adult / Child / Child, preschool / Female / Humans / Infant / Male Idioma: En Revista: Biol Blood Marrow Transplant Assunto da revista: HEMATOLOGIA / TRANSPLANTE Ano de publicação: 2015 Tipo de documento: Article