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piggyBac transposons expressing full-length human dystrophin enable genetic correction of dystrophic mesoangioblasts.
Loperfido, Mariana; Jarmin, Susan; Dastidar, Sumitava; Di Matteo, Mario; Perini, Ilaria; Moore, Marc; Nair, Nisha; Samara-Kuko, Ermira; Athanasopoulos, Takis; Tedesco, Francesco Saverio; Dickson, George; Sampaolesi, Maurilio; VandenDriessche, Thierry; Chuah, Marinee K.
Afiliação
  • Loperfido M; Department of Gene Therapy & Regenerative Medicine, Free University of Brussels, Brussels 1090, Belgium Center for Molecular & Vascular Biology, Department of Cardiovascular Sciences, University of Leuven, Leuven 3000, Belgium.
  • Jarmin S; School of Biological Sciences, Royal Holloway, University of London, Egham, Surrey, TW20 0EX, UK.
  • Dastidar S; Department of Gene Therapy & Regenerative Medicine, Free University of Brussels, Brussels 1090, Belgium.
  • Di Matteo M; Department of Gene Therapy & Regenerative Medicine, Free University of Brussels, Brussels 1090, Belgium Center for Molecular & Vascular Biology, Department of Cardiovascular Sciences, University of Leuven, Leuven 3000, Belgium.
  • Perini I; Translational Cardiomyology Laboratory, Embryo and Stem Cell Biology Unit, Department of Development and Regeneration, University of Leuven, Leuven 3000, Belgium.
  • Moore M; School of Biological Sciences, Royal Holloway, University of London, Egham, Surrey, TW20 0EX, UK.
  • Nair N; Department of Gene Therapy & Regenerative Medicine, Free University of Brussels, Brussels 1090, Belgium.
  • Samara-Kuko E; Department of Gene Therapy & Regenerative Medicine, Free University of Brussels, Brussels 1090, Belgium.
  • Athanasopoulos T; School of Biological Sciences, Royal Holloway, University of London, Egham, Surrey, TW20 0EX, UK Faculty of Science & Engineering, University of Wolverhampton, Wolverhampton, WV1 1LY, UK.
  • Tedesco FS; Department of Cell and Developmental Biology, University College London, London, WC1E 6DE, UK.
  • Dickson G; School of Biological Sciences, Royal Holloway, University of London, Egham, Surrey, TW20 0EX, UK.
  • Sampaolesi M; Translational Cardiomyology Laboratory, Embryo and Stem Cell Biology Unit, Department of Development and Regeneration, University of Leuven, Leuven 3000, Belgium.
  • VandenDriessche T; Department of Gene Therapy & Regenerative Medicine, Free University of Brussels, Brussels 1090, Belgium Center for Molecular & Vascular Biology, Department of Cardiovascular Sciences, University of Leuven, Leuven 3000, Belgium.
  • Chuah MK; Department of Gene Therapy & Regenerative Medicine, Free University of Brussels, Brussels 1090, Belgium Center for Molecular & Vascular Biology, Department of Cardiovascular Sciences, University of Leuven, Leuven 3000, Belgium marinee.chuah@vub.ac.be.
Nucleic Acids Res ; 44(2): 744-60, 2016 Jan 29.
Article em En | MEDLINE | ID: mdl-26682797

Texto completo: 1 Coleções: 01-internacional Base de dados: MEDLINE Assunto principal: Elementos de DNA Transponíveis / Terapia Genética / Distrofina / Distrofia Muscular de Duchenne Limite: Animals / Humans / Male Idioma: En Revista: Nucleic Acids Res Ano de publicação: 2016 Tipo de documento: Article País de afiliação: Bélgica

Texto completo: 1 Coleções: 01-internacional Base de dados: MEDLINE Assunto principal: Elementos de DNA Transponíveis / Terapia Genética / Distrofina / Distrofia Muscular de Duchenne Limite: Animals / Humans / Male Idioma: En Revista: Nucleic Acids Res Ano de publicação: 2016 Tipo de documento: Article País de afiliação: Bélgica