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Treatment-naïve Gaucher disease patients achieve therapeutic goals and normalization with velaglucerase alfa by 4years in phase 3 trials.
Zimran, Ari; Elstein, Deborah; Gonzalez, Derlis E; Lukina, Elena A; Qin, Yulin; Dinh, Quinn; Turkia, Hadhami Ben.
Afiliação
  • Zimran A; Gaucher Clinic, Shaare Zedek Medical Center, Hebrew University-Hadassah Medical School, Jerusalem, Israel. Electronic address: azimran@gmail.com.
  • Elstein D; Gaucher Clinic, Shaare Zedek Medical Center, Hebrew University-Hadassah Medical School, Jerusalem, Israel. Electronic address: delstein-c@shire.com.
  • Gonzalez DE; Instituto Privado de Hematología e Investigación Clínica (IPHIC), Asunción, Paraguay. Electronic address: gderlis@conexion.com.py.
  • Lukina EA; Department of Orphan Diseases, National Research Center for Hematology, Moscow, Russia. Electronic address: elenalukina02@gmail.com.
  • Qin Y; Shire, Lexington, MA, USA. Electronic address: yqin@shire.com.
  • Dinh Q; Shire, Lexington, MA, USA. Electronic address: qdinh@shire.com.
  • Turkia HB; Paediatric Department, La Rabta Hospital, Tunis, Tunisia. Electronic address: hadhami.baili@laposte.net.
Blood Cells Mol Dis ; 68: 153-159, 2018 02.
Article em En | MEDLINE | ID: mdl-27839979

Texto completo: 1 Coleções: 01-internacional Base de dados: MEDLINE Assunto principal: Doença de Gaucher / Glucosilceramidase Tipo de estudo: Clinical_trials Limite: Adolescent / Adult / Child / Female / Humans / Male / Middle aged Idioma: En Revista: Blood Cells Mol Dis Assunto da revista: HEMATOLOGIA Ano de publicação: 2018 Tipo de documento: Article

Texto completo: 1 Coleções: 01-internacional Base de dados: MEDLINE Assunto principal: Doença de Gaucher / Glucosilceramidase Tipo de estudo: Clinical_trials Limite: Adolescent / Adult / Child / Female / Humans / Male / Middle aged Idioma: En Revista: Blood Cells Mol Dis Assunto da revista: HEMATOLOGIA Ano de publicação: 2018 Tipo de documento: Article