Genetically Corrected iPSC-Derived Neural Stem Cell Grafts Deliver Enzyme Replacement to Affect CNS Disease in Sanfilippo B Mice.

Clarke, Don; Pearse, Yewande; Kan, Shih-Hsin; Le, Steven Q; Sanghez, Valentina; Cooper, Jonathan D; Dickson, Patricia I; Iacovino, Michelina

Clarke, Don; Pearse, Yewande; Kan, Shih-Hsin; Le, Steven Q; Sanghez, Valentina; Cooper, Jonathan D; Dickson, Patricia I; Iacovino, Michelina.

Afiliação

Clarke D; Department of Pediatrics, Los Angeles Biomedical Research Institute at Harbor-UCLA Medical Center, Torrance, CA 90502, USA.
Pearse Y; Phoenix Nest Inc., P.O. Box 150057, Brooklyn, NY 11215, USA.
Kan SH; Department of Pediatrics, Los Angeles Biomedical Research Institute at Harbor-UCLA Medical Center, Torrance, CA 90502, USA.
Le SQ; Department of Pediatrics, Los Angeles Biomedical Research Institute at Harbor-UCLA Medical Center, Torrance, CA 90502, USA.
Sanghez V; Department of Pediatrics, Los Angeles Biomedical Research Institute at Harbor-UCLA Medical Center, Torrance, CA 90502, USA.
Cooper JD; Department of Pediatrics, Los Angeles Biomedical Research Institute at Harbor-UCLA Medical Center, Torrance, CA 90502, USA.
Dickson PI; Department of Pediatrics, Los Angeles Biomedical Research Institute at Harbor-UCLA Medical Center, Torrance, CA 90502, USA.
Iacovino M; Department of Pediatrics, Los Angeles Biomedical Research Institute at Harbor-UCLA Medical Center, Torrance, CA 90502, USA.

Mol Ther Methods Clin Dev ; 10: 113-127, 2018 Sep 21.

Article em En | MEDLINE | ID: mdl-30101150

Palavras-chave

MPS IIIB; lysosomal storage disorder; stem cell therapy

Texto completo

Imprimir

XML

PubMed Links

Buscar no Google

Texto completo: 1 Coleções: 01-internacional Base de dados: MEDLINE Idioma: En Revista: Mol Ther Methods Clin Dev Ano de publicação: 2018 Tipo de documento: Article País de afiliação: Estados Unidos

Texto completo

Imprimir

XML

PubMed Links

Buscar no Google