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Gene replacement therapy in a model of Charcot-Marie-Tooth 4C neuropathy.
Schiza, Natasa; Georgiou, Elena; Kagiava, Alexia; Médard, Jean-Jacques; Richter, Jan; Tryfonos, Christina; Sargiannidou, Irene; Heslegrave, Amanda J; Rossor, Alexander M; Zetterberg, Henrik; Reilly, Mary M; Christodoulou, Christina; Chrast, Roman; Kleopa, Kleopas A.
Afiliação
  • Schiza N; Neuroscience Laboratory and Neurology Clinics, The Cyprus Institute of Neurology and Genetics and Cyprus School of Molecular Medicine, Nicosia, Cyprus.
  • Georgiou E; Neuroscience Laboratory and Neurology Clinics, The Cyprus Institute of Neurology and Genetics and Cyprus School of Molecular Medicine, Nicosia, Cyprus.
  • Kagiava A; Neuroscience Laboratory and Neurology Clinics, The Cyprus Institute of Neurology and Genetics and Cyprus School of Molecular Medicine, Nicosia, Cyprus.
  • Médard JJ; Department of Neuroscience and Department of Clinical Neuroscience, Karolinska Institutet, Stockholm, Sweden.
  • Richter J; Department of Molecular Virology, The Cyprus Institute of Neurology and Genetics and Cyprus School of Molecular Medicine, Nicosia, Cyprus.
  • Tryfonos C; Department of Molecular Virology, The Cyprus Institute of Neurology and Genetics and Cyprus School of Molecular Medicine, Nicosia, Cyprus.
  • Sargiannidou I; Neuroscience Laboratory and Neurology Clinics, The Cyprus Institute of Neurology and Genetics and Cyprus School of Molecular Medicine, Nicosia, Cyprus.
  • Heslegrave AJ; Department of Neurodegenerative Disease, UCL Institute of Neurology, London, UK.
  • Rossor AM; UK Dementia Research Institute at UCL, London, UK.
  • Zetterberg H; Department of Neuromuscular Diseases, UCL Institute of Neurology and National Hospital for Neurology and Neurosurgery, London, UK.
  • Reilly MM; Department of Neurodegenerative Disease, UCL Institute of Neurology, London, UK.
  • Christodoulou C; UK Dementia Research Institute at UCL, London, UK.
  • Chrast R; Department of Psychiatry and Neurochemistry, Institute of Neuroscience and Physiology, the Sahlgrenska Academy at the University of Gothenburg, Mölndal, Sweden.
  • Kleopa KA; Clinical Neurochemistry Laboratory, Sahlgrenska University Hospital, Mölndal, Sweden.
Brain ; 142(5): 1227-1241, 2019 05 01.
Article em En | MEDLINE | ID: mdl-30907403

Texto completo: 1 Coleções: 01-internacional Base de dados: MEDLINE Assunto principal: Terapia Genética / Doença de Charcot-Marie-Tooth / Peptídeos e Proteínas de Sinalização Intracelular / Modelos Animais de Doenças Tipo de estudo: Clinical_trials Limite: Animals / Humans Idioma: En Revista: Brain Ano de publicação: 2019 Tipo de documento: Article País de afiliação: Chipre

Texto completo: 1 Coleções: 01-internacional Base de dados: MEDLINE Assunto principal: Terapia Genética / Doença de Charcot-Marie-Tooth / Peptídeos e Proteínas de Sinalização Intracelular / Modelos Animais de Doenças Tipo de estudo: Clinical_trials Limite: Animals / Humans Idioma: En Revista: Brain Ano de publicação: 2019 Tipo de documento: Article País de afiliação: Chipre