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Targeted PMP22 TATA-box editing by CRISPR/Cas9 reduces demyelinating neuropathy of Charcot-Marie-Tooth disease type 1A in mice.
Lee, Ji-Su; Lee, Jae Y; Song, Dong W; Bae, Hee S; Doo, Hyun M; Yu, Ho S; Lee, Kyu J; Kim, Hee K; Hwang, Hyun; Kwak, Geon; Kim, Daesik; Kim, Seokjoong; Hong, Young B; Lee, Jung M; Choi, Byung-Ok.
Afiliação
  • Lee JS; Department of Health Sciences and Technology, SAIHST, Sungkyunkwan University, Seoul, 06351, Korea.
  • Lee JY; ToolGen, Inc., Seoul, 08501, Korea.
  • Song DW; ToolGen, Inc., Seoul, 08501, Korea.
  • Bae HS; ToolGen, Inc., Seoul, 08501, Korea.
  • Doo HM; Department of Health Sciences and Technology, SAIHST, Sungkyunkwan University, Seoul, 06351, Korea.
  • Yu HS; ToolGen, Inc., Seoul, 08501, Korea.
  • Lee KJ; ToolGen, Inc., Seoul, 08501, Korea.
  • Kim HK; Department of Neurology, Samsung Medical Center, Sungkyunkwan University School of Medicine, Seoul, 06351, Korea.
  • Hwang H; Department of Neurology, Samsung Medical Center, Sungkyunkwan University School of Medicine, Seoul, 06351, Korea.
  • Kwak G; Department of Health Sciences and Technology, SAIHST, Sungkyunkwan University, Seoul, 06351, Korea.
  • Kim D; Center for Genome Engineering, Institute for Basic Science (IBS), Seoul, 08826, Korea.
  • Kim S; Department of Chemistry, Seoul National University, Seoul, 08826, Korea.
  • Hong YB; ToolGen, Inc., Seoul, 08501, Korea.
  • Lee JM; Department of Biochemistry, College of Medicine, Dong-A University, Busan 49201, Korea.
  • Choi BO; School of Life Science, Handong Global University, Pohang 37554, Korea.
Nucleic Acids Res ; 48(1): 130-140, 2020 01 10.
Article em En | MEDLINE | ID: mdl-31713617

Texto completo: 1 Coleções: 01-internacional Base de dados: MEDLINE Assunto principal: Células de Schwann / Doença de Charcot-Marie-Tooth / TATA Box / Terapia de Alvo Molecular / Proteínas da Mielina / Bainha de Mielina Limite: Animals / Humans Idioma: En Revista: Nucleic Acids Res Ano de publicação: 2020 Tipo de documento: Article

Texto completo: 1 Coleções: 01-internacional Base de dados: MEDLINE Assunto principal: Células de Schwann / Doença de Charcot-Marie-Tooth / TATA Box / Terapia de Alvo Molecular / Proteínas da Mielina / Bainha de Mielina Limite: Animals / Humans Idioma: En Revista: Nucleic Acids Res Ano de publicação: 2020 Tipo de documento: Article