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Busulfan Pharmacokinetics in Adenosine Deaminase-Deficient Severe Combined Immunodeficiency Gene Therapy.
Bradford, Kathryn L; Liu, Siyu; Krajinovic, Maja; Ansari, Marc; Garabedian, Elizabeth; Tse, John; Wang, Xiaoyan; Shaw, Kit L; Gaspar, H Bobby; Candotti, Fabio; Kohn, Donald B.
Afiliação
  • Bradford KL; Department of Pediatric Hematology/Oncology, David Geffen School of Medicine at UCLA, Los Angeles, California.
  • Liu S; Department of Population Sciences, City of Hope/Beckman Research Institute, Duarte, California; Department of Hematology and Hematopoietic Cell Transplantation, City of Hope/Beckman Research Institute, Duarte, California.
  • Krajinovic M; Department of Pediatrics, University of Montreal, Montreal, Quebec, Canada; Department of Pharmacology and Physiology, University of Montreal, Montreal, Quebec, Canada.
  • Ansari M; Hematology-Oncology Unit, Department of Pediatrics, Geneva University Hospital & CANSEARCH Research Laboratory, University of Geneva, Geneva, Switzerland.
  • Garabedian E; Genetics and Molecular Biology Branch, National Human Genome Research Institute, National Institutes of Health, Bethesda, Maryland.
  • Tse J; Department of Pharmaceutical Services, Ronald Reagan Medical Center, UCLA, Los Angeles, California.
  • Wang X; Department of General Internal Medicine and Health Services Research, UCLA Health, Los Angeles, California.
  • Shaw KL; Department of Microbiology, Immunology and Molecular Genetics, University of California, Los Angeles, California.
  • Gaspar HB; UCL Great Ormond Street Institute of Child Health, London, United Kingdom; Orchard Therapeutics, London, United Kingdom.
  • Candotti F; Genetics and Molecular Biology Branch, National Human Genome Research Institute, National Institutes of Health, Bethesda, Maryland; Division of Immunology and Allergy, Lausanne University Hospital, Lausanne, Switzerland.
  • Kohn DB; Department of Pediatric Hematology/Oncology, David Geffen School of Medicine at UCLA, Los Angeles, California; Department of Microbiology, Immunology and Molecular Genetics, University of California, Los Angeles, California; Department of Molecular and Medical Pharmacology, David Geffen School of Me
Biol Blood Marrow Transplant ; 26(10): 1819-1827, 2020 10.
Article em En | MEDLINE | ID: mdl-32653625

Texto completo: 1 Coleções: 01-internacional Base de dados: MEDLINE Assunto principal: Imunodeficiência Combinada Severa / Transplante de Células-Tronco Hematopoéticas Tipo de estudo: Prognostic_studies Limite: Child / Humans / Infant Idioma: En Revista: Biol Blood Marrow Transplant Assunto da revista: HEMATOLOGIA / TRANSPLANTE Ano de publicação: 2020 Tipo de documento: Article

Texto completo: 1 Coleções: 01-internacional Base de dados: MEDLINE Assunto principal: Imunodeficiência Combinada Severa / Transplante de Células-Tronco Hematopoéticas Tipo de estudo: Prognostic_studies Limite: Child / Humans / Infant Idioma: En Revista: Biol Blood Marrow Transplant Assunto da revista: HEMATOLOGIA / TRANSPLANTE Ano de publicação: 2020 Tipo de documento: Article